Natural History Study of Children With Metachromatic Leukodystrophy

TerminatedOBSERVATIONAL
Enrollment

1

Participants

Timeline

Start Date

November 2, 2015

Primary Completion Date

April 8, 2016

Study Completion Date

April 8, 2016

Conditions
Lipid Metabolism DisordersMetachromatic Leukodystrophy (MLD)Nervous System DiseasesBrain DiseasesCentral Nervous System DiseasesDemyelinating DiseasesMetabolism, Inborn ErrorsGenetic Diseases, InbornSphingolipidosesHereditary Central Nervous System Demyelinating DiseasesMetabolic Inborn Brain DiseasesLysosomal Storage DiseasesMetabolic DiseasesSulfatidosis
Trial Locations (14)

2100

Copenhagen University Hospital, Rigshospitalet, Copenhagen

2650

Universitair Ziekenhuis Antwerpen (UZA) (University Hospital Antwerpen), Edegem

6100

Hacettepe Universitesi Tip Fakultesi Onkoloji Hastanesi, Ankara

15224

Children's Hospital Of Pittsburgh, Pittsburgh

20010

Children's National Health System, Washington D.C.

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

72076

Univesitatsklinikum Tubingen Klinik fur Kinder und Jugendmedizin, Tübingen

90502

Harbor UCLA Pediatrics, Torrance

94275

Hôpital De Bicêtre, Le Kremlin-Bicêtre

B1629ODT

Hospital Universitario Austral, Pilar

90035-003

Hospital de Cllnicas de Porto Alegre (HCPA) / UFRGS, Porto Alegre

H3Z 2Z3

Montreal Children's Hospital, Westmount

565-0871

Faculty Of Medicine, Osaka University Graduate School Of Medicine, Osaka

105-8461

The Jikei University School Of Medicine - Institute Of Dna Medicine, Tokyo

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Shire

INDUSTRY