EPI-743 in Friedreich's Ataxia Point Mutations

PHASE2CompletedINTERVENTIONAL
Enrollment

4

Participants

Timeline

Start Date

October 31, 2013

Primary Completion Date

June 30, 2016

Study Completion Date

June 30, 2016

Conditions
Friedreich's Ataxia
Interventions
DRUG

EPI-743

EPI-743 (alpha-tocotrienol quinone) is a small molecule therapeutic that was rationally designed to replete reduced glutathione through NQO1-catalyzed electron transfer from NADPH.

Trial Locations (1)

33612

University of South Florida, Tampa

Sponsors
All Listed Sponsors
collaborator

Edison Pharmaceuticals Inc

INDUSTRY

collaborator

Friedreich's Ataxia Research Alliance

OTHER

lead

University of South Florida

OTHER