70
Participants
Start Date
March 31, 2011
Primary Completion Date
September 30, 2014
Study Completion Date
September 30, 2014
Mayo Clinic, Rochester
Lead Sponsor
Rare Diseases Clinical Research Network
NETWORK
National Center for Advancing Translational Sciences (NCATS)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NIH
Mayo Clinic
OTHER