Efficacy and Safety Study of AeroVanc for the Treatment of Persistent MRSA Lung Infection in Cystic Fibrosis Patients

PHASE2CompletedINTERVENTIONAL
Enrollment

87

Participants

Timeline

Start Date

March 31, 2013

Primary Completion Date

November 30, 2014

Study Completion Date

November 30, 2014

Conditions
Cystic Fibrosis
Interventions
DRUG

Vancomycin hydrochloride inhalation powder

There will be two treatment cohorts in this study, each comprised of 40 randomized (1:1 active to placebo) and treated patients (adults ≥18 and children ≥12 years of age). In Cohort 1, patients will be enrolled and randomized to receive the 32 mg dose of AeroVanc bid or placebo bid. Prior to starting enrollment in Cohort 2, a safety evaluation will be carried out by the Data Monitoring Committee (DMC) based on treatment data from the first 20 patients in Cohort 1. Subject to the Sponsor's written communication of the DMC's opinion of acceptable safety, the dose for the active arm in Cohort 2 will be escalated to 64 mg bid. Optionally, the active arm for Cohort 2 may also be kept the same (32 mg bid), or reduced to 16 mg bid, depending on the outcome of the DMC's safety evaluation.

DRUG

Placebo inhalation powder

Trial Locations (38)

10032

Columbia University Medical Center, New York

11040

Hofstra North Shore - Long Island Jewish School of Medicine, New Hyde Park

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

19104

University of Pennsylvania, Philadelphia

27599

University of North Carolina, Chapel Hill

27710

Duke University Medical Center, Durham

29425

Medical University of South Carolina, Charleston

32803

Central Florida Pulmonary Group, Orlando

32806

Nemours Children's Clinic and Hospital, Orlando

33021

Joe DiMaggio Children's Hospital, Hollywood

33136

University of Miami - Miller School of Medicine, Miami

33606

New Lung Associates, PA; Lung Transplant, Adult Cystic Fibrosis, and the Center for Advanced Lung Diseases, Tampa General Hospital, Tampa

36608

Pulmonary Associates of Mobile, Mobile

37232

Vanderbilt University Medical Center, Nashville

40202

University of Louisville, Louisville

40536

University of Kentucky Cystic Fibrosis Clinic, Lexington

43205

Nationwide Children's Hospital, Columbus

44106

Rainbow Babies and Children's Hospital / University Hospitals Case Medical Center, Cleveland

45404

The Children's Medical Center of Dayton, Dayton

48201

Wayne State University, Harper Hospital, Children's Hospital of Michigan, Detroit

60025

The Cystic Fibrosis Center of Chicago, Glenview

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

Northwestern University Feinberg School of Medicine, Chicago

63110

Washington University School of Medicine, St Louis

66160

University of Kansas Medical Center, Kansas City

72205

University of Arkansas for Medical Science, Little Rock

73112

Santiago Reyes, MD, Oklahoma City

75390

University of Texas Southwestern Medical Center, Dallas

75708

University of Texas Health Science Center at Tyler, Tyler

77030

Baylor College of Medicine and Texas Children's Hospital, Houston

78723

Dell Children's Medical Center of Central Texas, Austin

80206

National Jewish Health, Denver

84132

University of Utah, Intermountain Cystic Fibrosis Center, Salt Lake City

90027

Children's Hospital Los Angeles, Division of Pediatric Pulmonology, Los Angeles

98195

University of Washington Medical Center, Seattle

02114

Massachusetts General Hospital Pediatric Cystic Fibrosis Center, Boston

02115

Boston Children's Hospital Cystic Fibrosis Center, Boston

08901

Rutgers Robert Wood Johnson Medical School, New Brunswick

All Listed Sponsors
collaborator

Synteract, Inc.

INDUSTRY

collaborator

Cystic Fibrosis Foundation

OTHER

lead

Savara Inc.

INDUSTRY

NCT01746095 - Efficacy and Safety Study of AeroVanc for the Treatment of Persistent MRSA Lung Infection in Cystic Fibrosis Patients | Biotech Hunter | Biotech Hunter