Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA

TerminatedOBSERVATIONAL
Enrollment

3

Participants

Timeline

Start Date

June 30, 2012

Primary Completion Date

February 28, 2013

Study Completion Date

February 28, 2013

Conditions
Mucopolysaccharidosis Type IVA
Trial Locations (1)

30033

Emory University, Dept of Human Genetics, Decatur

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

BioMarin Pharmaceutical

INDUSTRY

lead

Emory University

OTHER