A Natural History Study of Patients With GNE Myopathy and GNE-Related Diseases

RecruitingOBSERVATIONAL
Enrollment

125

Participants

Timeline

Start Date

September 14, 2011

Conditions
GNE MyopathyGNE Related Diseases
Trial Locations (1)

20892

RECRUITING

National Institutes of Health Clinical Center, Bethesda

All Listed Sponsors
collaborator

Therapeutics for Rare and Neglected Diseases (TRND)

NIH

lead

National Human Genome Research Institute (NHGRI)

NIH

NCT01417533 - A Natural History Study of Patients With GNE Myopathy and GNE-Related Diseases | Biotech Hunter | Biotech Hunter