5,000
Participants
Start Date
April 1, 2010
Primary Completion Date
December 31, 2026
Study Completion Date
December 31, 2026
RECRUITING
University of Westmead, Sydney
RECRUITING
University of Rochester, Rochester
RECRUITING
Children's Hospital of Philadelphia, Philadelphia
RECRUITING
University of Pennsylvania, Philadelphia
RECRUITING
Children's National Hospital, Washington D.C.
RECRUITING
Johns Hopkins University, Baltimore
RECRUITING
Nemours Children's Health, Orlando
RECRUITING
Nemours Children's Hospital, Orlando
RECRUITING
University of Miami, Miami
NOT_YET_RECRUITING
University of Michigan, Ann Arbor
RECRUITING
University of Iowa, Iowa City
RECRUITING
University of Minnesota, Minneapolis
RECRUITING
University of Colorado Hospital, Aurora
RECRUITING
Cedars-Sinai Medical Center, Los Angeles
RECRUITING
Stanford University, Palo Alto
NOT_YET_RECRUITING
Seattle Children's Hospital, Seattle
RECRUITING
University of Connecticut/Connecticut Children's Medical Center, Hartford
RECRUITING
Harvard/Massachusetts General Hospital, Boston
RECRUITING
St. Jude Children's Research Hospital, Memphis
RECRUITING
The Hospital for Sick Children, Toronto
RECRUITING
C. Besta Neurological Institute, Milan
RECRUITING
National Hospital of Neurology and Neurosurgery, London
Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta
OTHER
Johns Hopkins University
OTHER
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
King's College Hospital NHS Trust
OTHER
Nemours Children's Hospital
OTHER
Stanford University
OTHER
University of Pennsylvania
OTHER
University of Rochester
OTHER
Children's Hospital of Philadelphia
OTHER
Sydney Children's Hospitals Network
OTHER
Rare Diseases Clinical Research Network
NETWORK
Muscular Dystrophy Association
OTHER
National Institutes of Health (NIH)
NIH
Charcot-Marie-Tooth Association
OTHER
Massachusetts General Hospital
OTHER
Cedars-Sinai Medical Center
OTHER
University of Miami
OTHER
University of Minnesota
OTHER
Connecticut Children's Medical Center
OTHER
University of Colorado, Denver
OTHER
The National Hospital for Neurology and Neurosurgery
UNKNOWN
Dubowitz Neuromuscular Centre
OTHER
Michael Shy
OTHER