Observational Study on the Long Term Safety of Kuvan® Treatment in Patients With Hyperphenylalaninemia (HPA) Due to Phenylketonuria (PKU) or BH4 Deficiency

CompletedOBSERVATIONAL
Enrollment

627

Participants

Timeline

Start Date

December 31, 2009

Primary Completion Date

May 31, 2021

Study Completion Date

May 31, 2021

Conditions
Hyperphenylalaninemia (HPA) Due to Phenylketonuria (PKU) or Tetrahydrobiopterin (BH4) Deficiency
Trial Locations (69)

Unknown

Research Site, Graz

Research Site, Innsbruck

Research Site, Salzburg

Research Site, Vienna

Research Site, Amiens

Research Site, Angers

Research Site, Bordeaux

Research Site, Brest

Research Site, Bron

Research Site, Caen

Research Site, Dijon

Research Site, Lille

Research Site, Limoges

Research Site, Marseille

Research Site, Nantes

Research Site, Nice

Research Site - Armand Trousseau, Paris

Research Site - Necker, Paris

Research Site, Reims

Research Site, Rouen

Research Site, Strasbourg

Research Site, Tarbes

Research Site, Toulouse

Research Site, Tours

Research Site, Vandœuvre-lès-Nancy

Research Site, Berlin

Research Site, Cottbus

Research Site, Düsseldorf

Research Site, Frankfurt

Research Site, Hamburg

Research Site, Heidelberg

Research Site, Jena

Research Site, Leipzig

Research Site, Magdeburg

Research Site, München

Research Site, Münster

Research Site, Reutlingen

Research Site, Bologna

Research Site, Catania

Research Site, Catanzaro

Research Site, Genova

Research Site, Milan

Research Site - Ospedale Annunziata, Napoli

Research Site - Policlinico Federico, Napoli

Research Site, Padua

Research Site, Roma

Research Site, Amsterdam

Research Site, Groningen

Research Site, Maastricht

Research Site, Rotterdam

Research Site, Utrecht

Research Site, Porto

Research Site, Banská Bystrica

Research Site, Košice

Research Site, Bilbao

Research Site, Esplugues de Llobregat

Research Site, Madrid

Research Site, Málaga

Research Site, Murcia

Research Site, Palma de Mallorca

Research Site, Pamplona

Research Site, Santa Cruz de Tenerife

Research Site, Santander

Research Site, Santiago de Compostela

Research Site, Seville

Research Site, Zaragoza

Research Site, Gothenburg

Research Site, Stockholm

Research Site, Uppsala

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY