Gene Therapy for X-linked Chronic Granulomatous Disease (CGD) in Children

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

2

Participants

Timeline

Start Date

June 30, 2004

Primary Completion Date

December 31, 2010

Study Completion Date

September 30, 2011

Conditions
Chronic Granulomatous Disease
Interventions
GENETIC

retroviral SF71-gp91phox transduced CD34+ cells

autologous ex-vivo transduced (SF71-gp91phox)CD34+ cells

Trial Locations (1)

CH-8032

University Children's Hospital, Zurich

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Goethe University

OTHER

lead

University of Zurich

OTHER

NCT00927134 - Gene Therapy for X-linked Chronic Granulomatous Disease (CGD) in Children | Biotech Hunter | Biotech Hunter