1,887
Participants
Start Date
September 30, 2008
Primary Completion Date
January 29, 2021
Study Completion Date
January 29, 2021
Kuvan
-Recommended post-partum Assessments include: collection of baby's plasma at Birth, 1 Month and 6 months, and collection of mother's plasma and expressed breast milk sample at 1 Month.
Westchester Medical Center, Valhalla
Albany Medical Center, Albany
University of Rochester Medical Center, Rochester
Children's Hospital of Pittsburgh, Pittsburgh
Penn State, Milton S. Hershey Medical Center, Hershey
Children's Hospital of Philadelphia, Philadelphia
St. Christophers Hospital for Children, Philadelphia
Children's National Medical Center, Washington D.C.
Johns Hopkins University School of Medicine, Baltimore
Children's Hospital of the King's Daughters, Norfolk
West Virginia Genetics Center, Department of Pediatrics, Morgantown
University of North Carolina, Chapel Hill
Greenwood Genetic Center, Greenwood
Emory University, Decatur
University of Florida, Gainesville
University of Miami, Miller School of Medicine, Department of Human Genetics, Miami
University of South Florida, Tampa
Tampa Children's Hospital, St. Joseph's Pediatric Endocrine Associates, Tampa
Kosair Charities Pediatric Clinical Research Unit, Louisville
University of Kentucky, Lexington
Nationwide Children's Hospital, Columbus
Akron Children's Hospital, Akron
Indiana University School of Medicine, Indianapolis
University of Iowa, Iowa City
Children's Hospital of Wisconsin, Milwaukee
University of Minnesota, Minneapolis
Sanford Children's Specialty Clinic, Sioux Falls
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
St. Louis Children's Hospital, St Louis
University of Missouri Health Care, Columbia
Wesley Pediatric Faculty Clinic, Wichita
University of Nebraska, Omaha
Tulane University Medical School, New Orleans
University of Oklahoma, Oklahoma City
Children's Hospital, University of Colorado School of Medicine, Aurora
University of Utah, Salt Lake City
Childrens Hospital of Los Angeles, Los Angeles
LAC and USC Medical Center, Los Angeles
UCLA, Los Angeles
University of California, San Diego, San Diego
Children's Hospital of Orange County, Orange
Stanford University, Pediatrics, Stanford
Oregon Health and Science University, Portland
Children's Hosptial of Boston, Boston
AHS Hospital Corp, Morristown
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY