52
Participants
Start Date
December 31, 2010
Primary Completion Date
March 1, 2027
Study Completion Date
March 1, 2027
RECRUITING
University of Minnesota - Pediatric Genetics and Metabolism, Minneapolis
Rare Diseases Clinical Research Network
NETWORK
National Center for Advancing Translational Sciences (NCATS)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NIH
Lysosomal Disease Network
OTHER
University of Minnesota
OTHER