Baclofen Treatment of Ataxia Telangiectasia

EARLY_PHASE1CompletedINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

April 30, 2007

Primary Completion Date

February 28, 2011

Study Completion Date

February 28, 2011

Conditions
Ataxia Telangiectasia
Interventions
DRUG

Baclofen

Drug given by orally via capsules. Escalation steps in 4-day intervals. Step 1: 5mg QAM. Step 2: 5mg BID. Step 3: 5mg TID. Step 4: 10mg QAM, 5mg BID. Step 5: 10mg BID, 5mg QMid-day. Step 6: 10mg TID. Step 6 will last up to 2 weeks. De-escalation will start from highest dose step and work backwards in 2-day intervals. Complete drug administration of escalating, staying constant at 10mg TID and de-escalating will be done with both drug and placebo.

DRUG

Placebo

placebo drug

Trial Locations (2)

21108

Johns Hopkins Hospital, Baltimore

21287

Johns Hopkins Hospital, Baltimore

All Listed Sponsors
lead

Johns Hopkins University

OTHER

NCT00640003 - Baclofen Treatment of Ataxia Telangiectasia | Biotech Hunter | Biotech Hunter