Hematopoietic Stem Cell Transplantation for Treatment of Patients With Fanconi Anemia Lacking a Genotypically Identical Donor, Using Total Body Irradiation, Cyclophosphamide and Fludarabine

NACompletedINTERVENTIONAL
Enrollment

21

Participants

Timeline

Start Date

June 30, 2001

Primary Completion Date

May 31, 2013

Study Completion Date

May 31, 2013

Conditions
Fanconi Anemia
Interventions
DRUG

Cyclophosphamide

Cyclophosphamide (10mg/kg/day x 4days)

DRUG

Fludarabine

Fludarabine (30mg/m\^2/day x 5 days)

RADIATION

Total body irradiation (TBI)

TBI (450 cGY in a single fraction)

Trial Locations (1)

10065

Memorial Sloan Kettering Cancer Center, New York

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

National Cancer Institute (NCI)

NIH

collaborator

Miltenyi Biotec, Inc.

INDUSTRY

lead

Memorial Sloan Kettering Cancer Center

OTHER