4
Participants
Start Date
August 31, 2007
Primary Completion Date
December 31, 2017
Study Completion Date
December 31, 2017
Hemophilia Center of Western Pennsylvania, Pittsburgh
Children's Hospital of Philadelphia, Philadelphia
Children's Hospital of Philadelphia
OTHER
The Hemophilia Center of Western Pennsylvania
OTHER
Royal Prince Alfred Hospital, Sydney, Australia
OTHER
Spark Therapeutics, Inc.
INDUSTRY