130
Participants
Start Date
April 30, 2007
Primary Completion Date
November 30, 2013
Study Completion Date
November 30, 2013
Mount Sinai School of Medicine, New York
University of Lyon, Lyon
University of Texas Southwestern Medical Center, Dallas
University of Sao Paulo, São Paulo
Office of Rare Diseases (ORD)
NIH
Rare Diseases Clinical Research Network
NETWORK
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
NIH
Icahn School of Medicine at Mount Sinai
OTHER