89
Participants
Start Date
December 31, 2006
Primary Completion Date
September 30, 2010
Study Completion Date
February 28, 2011
Sirolimus
A sirolimus dose of 2 tablets (1 mg/tablet) per day for 1 year.
Placebo
A placebo dose of 2 tablets per day for 1 year.
National Heart, Lung, and Blood Institute, Bethesda
Medical University of South Carolina, Charleston
University of Florida, Gainesville, Gainesville
Cleveland Clinic Foundation, Cleveland
University of Cincinnati Medical Center, Cincinnati
University of Texas Health Center at Tyler, Tyler
National Jewish Medical and Research Center, Denver
University of California Los Angeles, Los Angeles
Oregon Health & Science University, Portland
Harvard's Brigham and Women's Hospital, Boston
Toronto General Hospital, Toronto
National Kinki-Chou Hospital, Sakai
Niigata University Medical and Dental Hospital, Niigata
Office of Rare Diseases (ORD)
NIH
FDA Office of Orphan Products Development
FED
National Center for Research Resources (NCRR)
NIH
University of Cincinnati
OTHER