Measure Liver Fat Content After ISIS 301012 (Mipomersen) Administration

PHASE2CompletedINTERVENTIONAL
Enrollment

38

Participants

Timeline

Start Date

July 31, 2006

Primary Completion Date

March 31, 2010

Study Completion Date

September 30, 2010

Conditions
Lipid Metabolism, Inborn ErrorsHyperlipidemiasMetabolic DiseasesHypolipoproteinemiaHypolipoproteinemiasHypobetalipoproteinemiasMetabolism, Inborn ErrorsGenetic Diseases, InbornInfant, Newborn, DiseasesCongenital AbnormalitiesMetabolic DisorderHypercholesterolemiaDyslipidemiasLipid Metabolism Disorders
Interventions
DRUG

mipomersen

200 mg subcutaneous injections

DRUG

Placebo

subcutaneous injections

Trial Locations (1)

1105 AZ

Amsterdam

Sponsors
All Listed Sponsors
collaborator

Ionis Pharmaceuticals, Inc.

INDUSTRY

lead

Kastle Therapeutics, LLC

INDUSTRY