International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

RecruitingOBSERVATIONAL
Enrollment

12,000

Participants

Timeline

Start Date

April 1, 1991

Primary Completion Date

January 31, 2034

Study Completion Date

January 31, 2034

Conditions
Gaucher DiseaseCerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency DiseaseGlucosylceramide Beta-Glucosidase Deficiency Disease
Trial Locations (315)

100

RECRUITING

Investigational Site Number : 151182, Taipei

112

RECRUITING

Investigational Site Number : 152226, Taipei

261

RECRUITING

Investigational Site Number : 4000001, Amman

333

RECRUITING

Investigational Site Number : 153158, Taoyuan

404

RECRUITING

Investigational Site Number : 151179, Taichung

704

RECRUITING

Investigational Site Number : 153248, Tainan City

710

RECRUITING

Investigational Site Number : 152153, Tainan City

807

COMPLETED

Investigational Site Number : 152244, Kaohsiung City

833

RECRUITING

Investigational Site Number : 152246, Kaohsiung City

1000

RECRUITING

Investigational Site Number : 608001, Manila

1020

RECRUITING

Investigational Site Number : 151796, Brussels

1090

RECRUITING

Investigational Site Number : 150944, Brussels

RECRUITING

Investigational Site Number : 152345, Brussels

1123

COMPLETED

Investigational Site Number : 151085, Sarandí

1200

RECRUITING

Investigational Site Number : 150517, Brussels

1425

RECRUITING

Investigational Site Number : 150661, CABA

RECRUITING

Investigational Site Number : 032012, Buenos Aires

1680

RECRUITING

Investigational Site Number : 100001, Sofia

1900

RECRUITING

Investigational Site Number : 032003, La Plata

2000

RECRUITING

Investigational Site Number : 154138, Johannesburg

2020

RECRUITING

Investigational Site Number : 150722, Antwerp

2050

TERMINATED

Investigational Site Number : 151431, Sydney

2100

RECRUITING

Investigational Site Number : 151229, København Ø

2115

RECRUITING

Boston Children's Hospital- Site Number : 840092, Boston

2145

RECRUITING

Investigational Site Number : 151069, Westmead

2196

RECRUITING

Investigational Site Number : 150346, Sandton

2650

RECRUITING

Investigational Site Number : 154285, Edegem

3000

RECRUITING

Investigational Site Number : 151668, Leuven

3010

RECRUITING

Investigational Site Number : 157045, Bern

3050

RECRUITING

Investigational Site Number : 151008, Parkville

3168

RECRUITING

Investigational Site Number : 151011, Clayton

3400

COMPLETED

Investigational Site Number : 154176, Corrientes

4029

COMPLETED

Investigational Site Number : 151010, Brisbane

4281

RECRUITING

Investigational Site Number : 3480003, Létavértes

4400

RECRUITING

Investigational Site Number : 3480007, Nyíregyháza

4810

COMPLETED

Investigational Site Number : 151491, Douglas

5000

RECRUITING

Investigational Site Number : 151002, Adelaide

5001

RECRUITING

Investigational Site Number : 157237, Aarau

6150

RECRUITING

Investigational Site Number : 151015, Murdoch

7000

RECRUITING

Investigational Site Number : 151725, Hobart

8000

TERMINATED

Investigational Site Number : 151156, Bruges

RECRUITING

Investigational Site Number : 3480008, Székesfehérvár

8091

RECRUITING

Investigational Site Number : 157241, Zurich

9000

COMPLETED

Investigational Site Number : 151134, Ghent

10000

RECRUITING

Investigational Site Number : 1910001, Zagreb

RECRUITING

Investigational Site Number : 1910002, Zagreb

RECRUITING

Investigational Site Number : 1910003, Zagreb

10016

RECRUITING

New York University School Of Medicine- Site Number : 840040, New York

10019

RECRUITING

Columbia University Medical Center - New York- Site Number : 840125, New York

10029

RECRUITING

Mt. Sinai School of Medicine- Site Number : 840005, New York

10101

RECRUITING

Investigational Site Number : 2140001, Santo Domingo

10400

RECRUITING

Investigational Site Number : 764003, Bangkok

10449

RECRUITING

Investigational Site Number : 152321, Taipei

10595

RECRUITING

New York Medical College- Site Number : 840039, Valhalla

10700

RECRUITING

Investigational Site Number : 764004, Bangkok

11000

RECRUITING

Investigational Site Number : 688001, Belgrade

RECRUITING

Investigational Site Number : 688002, Belgrade

RECRUITING

Investigational Site Number : 688003, Belgrade

RECRUITING

Investigational Site Number : 688005, Belgrade

11030

RECRUITING

Northwell Health- Site Number : 840102, Manhasset

11527

RECRUITING

Investigational Site Number : 300002, Athens

11566

RECRUITING

Investigational Site Number : 9829, Cairo

12808

RECRUITING

Investigational Site Number : 150809, Prague

13210

RECRUITING

State University of New York- Site Number : 840052, Syracuse

13285

TERMINATED

Investigational Site Number : 250011, Marseille

13353

RECRUITING

Investigational Site Number : 151686, Berlin

14033

COMPLETED

Investigational Site Number : 250002, Caen

14642

RECRUITING

University of Rochester Medical Center SOM- Site Number : 840105, Rochester

15006

COMPLETED

Investigational Site Number : 154146, A Coruña

15224

RECRUITING

University of Pittsburgh- Site Number : 840023, Pittsburgh

16147

RECRUITING

Investigational Site Number : 380006, Genova

17033

RECRUITING

Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey

18000

RECRUITING

Investigational Site Number : 688004, Niš

19104

RECRUITING

Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia

20010

RECRUITING

Children's National Medical Center- Site Number : 840067, Washington D.C.

20099

RECRUITING

Investigational Site Number : 151369, Hamburg

20122

RECRUITING

Investigational Site Number : 380004, Milan

20246

COMPLETED

Investigational Site Number : 151368, Hamburg

20502

ACTIVE_NOT_RECRUITING

Investigational Site Number : 151726, Malmo

20900

RECRUITING

Investigational Site Number : 380002, Monza (MB)

21955

RECRUITING

Investigational Site Number : 682004, Mecca

22030

RECRUITING

O&O Alpan, LLC- Site Number : 840025, Fairfax

22908

COMPLETED

University of Virginia School of Medicine-Pediatrics- Site Number : 840078, Charlottesville

23142

RECRUITING

Investigational Site Number : 151534, New Taipei City

23507

COMPLETED

Children's Hospital of the Kings Daughters- Site Number : 840072, Norfolk

25000

COMPLETED

Investigational Site Number : 250004, Besançon

26500

RECRUITING

Investigational Site Number : 300003, Pátrai

27710

RECRUITING

Duke University Medical Center Genetics Dept- Site Number : 840037, Durham

28007

RECRUITING

Investigational Site Number : 154163, Madrid

RECRUITING

Investigational Site Number : 154236, Madrid

28034

RECRUITING

Investigational Site Number : 151524, Madrid

28040

TERMINATED

Investigational Site Number : 153251, Madrid

28041

RECRUITING

Investigational Site Number : 154199, Madrid

28046

RECRUITING

Investigational Site Number : 154160, Madrid

28232

RECRUITING

Carolinas Medical Center Hospital- Site Number : 840065, Charlotte

28922

RECRUITING

Investigational Site Number : 154119, Alcorcón

29200

RECRUITING

Investigational Site Number : 250005, Brest

29605

RECRUITING

Greenwood Genetcs- Site Number : 840055, Greenville

30033

RECRUITING

Emory University School of Medicine- Human Genetics- Site Number : 840060, Decatur

31027

COMPLETED

Investigational Site Number : 250017, Toulouse

32207

RECRUITING

University of Florida Pediatrics Genetics- Site Number : 840121, Jacksonville

32216

COMPLETED

The Atwal Clinic- Site Number : 840112, Jacksonville

33000

RECRUITING

Investigational Site Number : 250008, Bordeaux

33065

RECRUITING

University Hematology Oncology- Site Number : 840075, Coral Springs

33100

RECRUITING

Investigational Site Number : 380001, Udine

33136

RECRUITING

University Of Miami SOM- Site Number : 840006, Miami

33606

RECRUITING

University of Florida-Genetics- Site Number : 840096, Tampa

33612

COMPLETED

Pediatric Endocrine Associates- Site Number : 840017, Tampa

34295

RECRUITING

Investigational Site Number : 2500013, Montpellier

35128

RECRUITING

Investigational Site Number : 380003, Padua

35203

RECRUITING

Investigational Site Number : 250012, Rennes

35392

RECRUITING

Investigational Site Number : 154150, Giessen

36200

RECRUITING

Investigational Site Number : 153213, Vigo

36424

RECRUITING

Investigational Site Number : 682002, Al Mubarraz

37044

RECRUITING

Investigational Site Number : 250016, Tours

38232

RECRUITING

Vanderbilt University Hospital-Pediatrics- Site Number : 840049, Nashville

40002

RECRUITING

Investigational Site Number : 764005, Khon Kaen

40202

COMPLETED

University of Louisville- Genetics- Site Number : 840030, Louisville

40225

RECRUITING

Investigational Site Number : 150783, Düsseldorf

41013

RECRUITING

Investigational Site Number : 153215, Seville

RECRUITING

Investigational Site Number : 153219, Seville

41126

RECRUITING

Investigational Site Number : 380005, Modena

43017

RECRUITING

LSD Data Registry Site LLC- Site Number : 840094, Dublin

44093

RECRUITING

Investigational Site Number : 250006, Nantes

44106

RECRUITING

University Hospitals Cleveland Medical Center- Site Number : 840119, Cleveland

44195

RECRUITING

Cleveland Clinic Foundation Pediatrics- Site Number : 840048, Cleveland

46026

RECRUITING

Investigational Site Number : 154205, Valencia

46045

COMPLETED

Investigational Site Number : 150432, Oberhausen

46202

RECRUITING

Indianapolis University School of Medicine- Site Number : 840027, Indianapolis

48109

RECRUITING

University of Michigan Pediatrics- Site Number : 840107, Ann Arbor

48201

RECRUITING

Children's Hospital of Michigan- Site Number : 840066, Detroit

49503

COMPLETED

Spectrum for Health- Site Number : 840019, Grand Rapids

49525

COMPLETED

Infusion Associates- Site Number : 840050, Grand Rapids

50006

RECRUITING

Investigational Site Number : 154238, Zaragoza

50009

RECRUITING

Investigational Site Number : 153216, Zaragoza

50134

COMPLETED

Investigational Site Number : 380009, Florence

50586

RECRUITING

Investigational Site Number : 458001, Jalan Pahang

50612

TERMINATED

Investigational Site Number : 154208, Yangsan

52242

RECRUITING

University of Iowa- Site Number : 840032, Iowa City

53226

RECRUITING

Children's Hospital of Wisconsin-Pediatrics- Site Number : 840054, Milwaukee

55131

RECRUITING

Investigational Site Number : 150031, Mainz

55404

RECRUITING

Children's Health Care- Site Number : 840114, Minneapolis

RECRUITING

Children's Hospital and Clinics of Minnesota- Site Number : 840046, Minneapolis

55455

RECRUITING

University of Minnesota Medical Center Pediatrics- Site Number : 840076, Minneapolis

59100

RECRUITING

Investigational Site Number : 458002, Kuala Lumpur

60182

RECRUITING

Investigational Site Number : 154092, Norrköping

60611

RECRUITING

Ann and Robert Lurie Children's Hospital- Site Number : 840011, Chicago

RECRUITING

Ann and Robert Lurie Children's Hospital- Site Number : 840013, Chicago

60612

RECRUITING

Rush University Medical Center Genetics- Site Number : 840079, Chicago

63110

RECRUITING

Washington University of St. Louis- Site Number : 840100, St Louis

64108

COMPLETED

Children's Mercy Hospital- Pediatrics- Site Number : 840063, Kansas City

65212

RECRUITING

University of Missouri Health System Department of Genetics- Site Number : 840031, Columibia

67000

RECRUITING

Investigational Site Number : 250018, Strasbourg

68198

RECRUITING

University of Nebraska Medical Center- Pediatrics- Site Number : 840084, Omaha

69437

COMPLETED

Investigational Site Number : 250009, Lyon

69677

RECRUITING

Investigational Site Number : 250014, Bron

70112

COMPLETED

Tulane University Medical Center- Site Number : 840001, New Orleans

72202

RECRUITING

Arkansas Childrens Hospital- Site Number : 840109, Little Rock

72205

RECRUITING

University of Arkansas for Medical Sciences- Site Number : 840113, Little Rock

75013

TERMINATED

Investigational Site Number : 250007, Paris

75015

RECRUITING

Investigational Site Number : 250010, Paris

75226

RECRUITING

Baylor Research Center- Site Number : 840058, Dallas

76104

RECRUITING

Cook Children's Health Care System- Site Number : 840024, Fort Worth

80045

RECRUITING

University of Colorado at Denver Genetics- Site Number : 840068, Aurora

83340

COMPLETED

Investigational Site Number : 703001, Bratislava

84132

RECRUITING

University of Utah Department of Medical Genetics- Site Number : 840043, Salt Lake City

85013

RECRUITING

Phoenix Children's Hospital- Site Number : 840003, Phoenix

85724

RECRUITING

University of Arizona- Site Number : 840015, Tucson

89109

RECRUITING

Children's Specialty Center of Nevada- Site Number : 840008, Las Vegas

90027

RECRUITING

Southern California Permanente Medical Group- Site Number : 840108, Los Angeles

90033

COMPLETED

USC Health Sciences Center Dept of Genetics- Site Number : 840082, Los Angeles

90211

RECRUITING

Tower Hematology/Oncology Medical Group- Site Number : 840056, Beverly Hills

92093

COMPLETED

University of California at San Diego- Site Number : 840007, San Diego

92110

RECRUITING

Investigational Site Number : 250001, Clichy

92380

RECRUITING

Investigational Site Number : 250003, Garches

92617

RECRUITING

University of California at Irvine- Site Number : 840036, Irvine

92868

RECRUITING

Children's Hospital of Orange County- Site Number : 840074, Orange

94305

RECRUITING

Stanford Unviersity MC Dept of Genetics- Site Number : 840022, Palo Alto

95100

RECRUITING

Investigational Site Number : 380008, Catania

95817

RECRUITING

UC Davis MIND Institute- Site Number : 840010, Sacramento

95825

COMPLETED

Kaiser Permanente Hospital- Site Number : 840042, Sacramento

97239

RECRUITING

Oregon Health and Science University- Site Number : 840080, Portland

98105

RECRUITING

Seattle Children's Hospital- Site Number : 840028, Seattle

98195

RECRUITING

University Of Washington Medical Center- Site Number : 840059, Seattle

98415

RECRUITING

Multicare Health System ¿ Mary Bridge Childrens Hospital- Site Number : 840115, Tacoma

100045

TERMINATED

Investigational Site Number : 151787, Beijing

RECRUITING

Investigational Site Number : 1560001, Beijing

166830

RECRUITING

Investigational Site Number : 422001, Beirut

200092

TERMINATED

Investigational Site Number : 152356, Shanghai

229899

RECRUITING

Investigational Site Number : 702001, Singapore

302015

COMPLETED

Investigational Site Number : 356004, Jaipur

310003

TERMINATED

Investigational Site Number : 152358, Hangzhou

380015

RECRUITING

Investigational Site Number : 356003, Ahmedabad

400006

RECRUITING

Investigational Site Number : 642001, Cluj-Napoca

400025

RECRUITING

Investigational Site Number : 356005, Mumbai

400370

COMPLETED

Investigational Site Number : 151188, Cluj-Napoca

RECRUITING

Investigational Site Number : 642002, Cluj-Napoca

500026

RECRUITING

Investigational Site Number : 3560006, Secunderabad

510080

TERMINATED

Investigational Site Number : 152357, Guangzhou

RECRUITING

Investigational Site Number : 1560002, Guangzhou

632004

RECRUITING

Investigational Site Number : 356002, Vellore

700000

RECRUITING

Investigational Site Number : 704002, Ho Chi Minh City

700017

RECRUITING

Investigational Site Number : 356001, Kolkata

Unknown

RECRUITING

University of California at San Francisco- Site Number : 840051, San Francisco

COMPLETED

John Hopkins- Site Number : 840044, Baltimore

TERMINATED

Cooper Health Center- Site Number : 840098, Camden

RECRUITING

Site Number : 840026, New York

RECRUITING

Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia

RECRUITING

Investigational Site Number : 151164, Sofia

TERMINATED

Investigational Site Number : 156003, Beijing

TERMINATED

Investigational Site Number : 152359, Hangzhou

TERMINATED

Investigational Site Number : 150899, Shanghai

RECRUITING

Investigational Site Number : 170004, Bogotá

RECRUITING

Investigational Site Number : 818007, Al Mansurah

RECRUITING

Investigational Site Number : 5748, Alexandria

RECRUITING

Investigational Site Number : 9889, Ash Sharqia

RECRUITING

Investigational Site Number : 9888, Asyut

RECRUITING

Investigational Site Number : 8345, Cairo

RECRUITING

Investigational Site Number : 9830, Cairo

RECRUITING

Investigational Site Number : 300004, Athens

RECRUITING

Investigational Site Number : 344001, Kowloon

RECRUITING

Investigational Site Number : 360001, Jakarta

RECRUITING

Investigational Site Number : 3760003, Haifa

RECRUITING

Investigational Site Number : 3760001, Jerusalem

RECRUITING

Investigational Site Number : 3760002, Petah Tikva

RECRUITING

Investigational Site Number : 380011, Monza

RECRUITING

Investigational Site Number : 380010, Napoli

COMPLETED

Investigational Site Number : 154225, Kuwait City

RECRUITING

Investigational Site Number : 4220004, Beirut

COMPLETED

Investigational Site Number : 150149, Amsterdam

TERMINATED

Investigational Site Number : 151171, Amsterdam

RECRUITING

Investigational Site Number : 154264, Karachi

RECRUITING

Investigational Site Number : 154266, Lahore

RECRUITING

Investigational Site Number : 604001, Arequipa

RECRUITING

Investigational Site Number : 620003, Coimbra

RECRUITING

Investigational Site Number : 643001, Moscow

RECRUITING

Investigational Site Number : 643002, sait-Petersburg

COMPLETED

Investigational Site Number : 682003, Jeddah

RECRUITING

Investigational Site Number : 710-003, Johannesburg

RECRUITING

Investigational Site Number : 153191, Daejeon

RECRUITING

Investigational Site Number : 153212, Seoul

RECRUITING

Investigational Site Number : 153222, Seoul

RECRUITING

Investigational Site Number : 154093, Chiayi City

RECRUITING

Investigational Site Number : 152152, Hualien City

RECRUITING

Investigational Site Number : 151500, Putz City, Chia-yi

RECRUITING

Investigational Site Number : 764001, Bangkok

RECRUITING

Investigational Site Number : 792001, Ankara

RECRUITING

Investigational Site Number : 792002, Ankara

RECRUITING

Investigational Site Number : 792004, Istanbul

RECRUITING

Investigational Site Number : 792007, Izmir

RECRUITING

Investigational Site Number : 792003, Malatya

RECRUITING

Investigational Site Number : 7840001, Dubai

RECRUITING

Investigational Site Number : 154212, Hanoi

06520

RECRUITING

Yale - Site Number : 840047, New Haven

04102

RECRUITING

Maine Medical Center Pediatrics- Site Number : 840064, Portland

02114

RECRUITING

Massachusetts General Hospital-Genetics- Site Number : 840062, Boston

07601

RECRUITING

Joseph M. Sanzari Children's Hospital- Site Number : 840101, Hackensack

07962

RECRUITING

Atlantic Health System- Site Number : 840099, Morristown

08901

RECRUITING

St. Peter's University Hospital- Site Number : 840016, New Brunswick

07503

RECRUITING

St. Joseph's Children's Hospital- Site Number : 840057, Paterson

10029-7494

RECRUITING

Metropolitan Hospital Center- Site Number : 840110, New York

43205-2664

RECRUITING

Nationwide Children's Hospital- Site Number : 840091, Columbus

02903

COMPLETED

Rhode Island Hospital Genetics- Site Number : 840053, Providence

X5004FHP

RECRUITING

Investigational Site Number : 032011, Córdoba

80060-150

RECRUITING

Hospital das Clínicas da Universidade Federal do Paraná - HCUFPR- Site Number : 076010, Curitiba

90035-903

RECRUITING

Hospital de Clinicas de Porto Alegre- Site Number : 076007, Porto Alegre

13034-685

RECRUITING

Hospital e Maternidade Celso Pierro - PUC-Campinas- Site Number : 076012, Campinas

14049-900

RECRUITING

Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto- Site Number : 076001, Ribeirão Preto

13083-220

RECRUITING

Faculdade De Medicina - Unicamp- Site Number : 076005, Campinas

20211-030

RECRUITING

HEMORIO- Site Number : 076006, Rio de Janeiro

04020-041

RECRUITING

Instituto de Genética e Erros Inatos do Metabolismo- Site Number : 076002, São Paulo

05403-000

RECRUITING

Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 076008, São Paulo

T2E 7Z4

RECRUITING

Investigational Site Number : 124014, Calgary

TG62B7

RECRUITING

Investigational Site Number : 124002, Edmonton

V5Z1M9

RECRUITING

Investigational Site Number : 124010, Vancouver

V6H3N1

COMPLETED

Investigational Site Number : 124011, Vancouver

R3A1R9

RECRUITING

Investigational Site Number : 124019, Winnipeg

E1C 2Z3

RECRUITING

Investigational Site Number : 124022, Moncton

K7L 2V7

RECRUITING

Investigational Site Number : 124024, Kingston

K7L2V7

TERMINATED

Investigational Site Number : 124005, Kingston

N6A 5W9

RECRUITING

Investigational Site Number : 124021, London

M5G 1X8

RECRUITING

Investigational Site Number : 124006, Toronto

M5G1X5

RECRUITING

Investigational Site Number : 124013, Toronto

J1H5N4

RECRUITING

Investigational Site Number : 124001, Sherbrooke

546 42

RECRUITING

Investigational Site Number : 300001, Thessaloniki

H-1097

RECRUITING

Investigational Site Number : 3480006, Budapest

00161

RECRUITING

Investigational Site Number : 380007, Rome

07100

RECRUITING

Investigational Site Number : 380014, Sassari

545-8585

COMPLETED

Investigational Site Number : 153205, Abeno-ku

683-8504

COMPLETED

Investigational Site Number : 153203, Yonago-shi

266-0007

RECRUITING

Investigational Site Number : 153217, Chiba

157-8535

RECRUITING

Investigational Site Number : 153204, Tokyo

08661

RECRUITING

Investigational Site Number : 154237, Vilnius

Callao02

RECRUITING

Investigational Site Number : 604002, Callao

04-730

RECRUITING

Investigational Site Number : 150575, Warsaw

1649-035

RECRUITING

Investigational Site Number : 620004, Lisbon

9500-370

RECRUITING

Investigational Site Number : 620009, Ponta Delgada

03080

RECRUITING

Investigational Site Number : 153180, Seoul

RECRUITING

Investigational Site Number : 153196, Seoul

05505

RECRUITING

Investigational Site Number : 151149, Seoul

08035

RECRUITING

Investigational Site Number : 153237, Barcelona

RECRUITING

Investigational Site Number : 154147, Barcelona

08208

RECRUITING

Investigational Site Number : 154145, Sabadell

501 82

COMPLETED

Investigational Site Number : 154095, Borås

00407

RECRUITING

Investigational Site Number : 151181, Taichung

01330

RECRUITING

Investigational Site Number : 792006, Adana

06620

RECRUITING

Investigational Site Number : 792005, Ankara

CB2 2QQ

RECRUITING

Investigational Site Number : 151340, Cambridge

B15 2TH

RECRUITING

Investigational Site Number : 152287, Birmingham

NW1 2BU

RECRUITING

Investigational Site Number : 151646, London

WC1N 3JH

RECRUITING

Investigational Site Number : 150303, London

M6 8HD

RECRUITING

Investigational Site Number : 152361, Salford

B46NH

RECRUITING

Investigational Site Number : 154240, Birmingham

NW32QG

RECRUITING

Investigational Site Number : 151123, London

M13 0JE

RECRUITING

Investigational Site Number : 150455, Manchester

All Listed Sponsors
lead

Genzyme, a Sanofi Company

INDUSTRY