12,000
Participants
Start Date
April 1, 1991
Primary Completion Date
January 31, 2034
Study Completion Date
January 31, 2034
RECRUITING
Investigational Site Number : 151182, Taipei
RECRUITING
Investigational Site Number : 152226, Taipei
RECRUITING
Investigational Site Number : 4000001, Amman
RECRUITING
Investigational Site Number : 153158, Taoyuan
RECRUITING
Investigational Site Number : 151179, Taichung
RECRUITING
Investigational Site Number : 153248, Tainan City
RECRUITING
Investigational Site Number : 152153, Tainan City
COMPLETED
Investigational Site Number : 152244, Kaohsiung City
RECRUITING
Investigational Site Number : 152246, Kaohsiung City
RECRUITING
Investigational Site Number : 608001, Manila
RECRUITING
Investigational Site Number : 151796, Brussels
RECRUITING
Investigational Site Number : 150944, Brussels
RECRUITING
Investigational Site Number : 152345, Brussels
COMPLETED
Investigational Site Number : 151085, Sarandí
RECRUITING
Investigational Site Number : 150517, Brussels
RECRUITING
Investigational Site Number : 150661, CABA
RECRUITING
Investigational Site Number : 032012, Buenos Aires
RECRUITING
Investigational Site Number : 100001, Sofia
RECRUITING
Investigational Site Number : 032003, La Plata
RECRUITING
Investigational Site Number : 154138, Johannesburg
RECRUITING
Investigational Site Number : 150722, Antwerp
TERMINATED
Investigational Site Number : 151431, Sydney
RECRUITING
Investigational Site Number : 151229, København Ø
RECRUITING
Boston Children's Hospital- Site Number : 840092, Boston
RECRUITING
Investigational Site Number : 151069, Westmead
RECRUITING
Investigational Site Number : 150346, Sandton
RECRUITING
Investigational Site Number : 154285, Edegem
RECRUITING
Investigational Site Number : 151668, Leuven
RECRUITING
Investigational Site Number : 157045, Bern
RECRUITING
Investigational Site Number : 151008, Parkville
RECRUITING
Investigational Site Number : 151011, Clayton
COMPLETED
Investigational Site Number : 154176, Corrientes
COMPLETED
Investigational Site Number : 151010, Brisbane
RECRUITING
Investigational Site Number : 3480003, Létavértes
RECRUITING
Investigational Site Number : 3480007, Nyíregyháza
COMPLETED
Investigational Site Number : 151491, Douglas
RECRUITING
Investigational Site Number : 151002, Adelaide
RECRUITING
Investigational Site Number : 157237, Aarau
RECRUITING
Investigational Site Number : 151015, Murdoch
RECRUITING
Investigational Site Number : 151725, Hobart
TERMINATED
Investigational Site Number : 151156, Bruges
RECRUITING
Investigational Site Number : 3480008, Székesfehérvár
RECRUITING
Investigational Site Number : 157241, Zurich
COMPLETED
Investigational Site Number : 151134, Ghent
RECRUITING
Investigational Site Number : 1910001, Zagreb
RECRUITING
Investigational Site Number : 1910002, Zagreb
RECRUITING
Investigational Site Number : 1910003, Zagreb
RECRUITING
New York University School Of Medicine- Site Number : 840040, New York
RECRUITING
Columbia University Medical Center - New York- Site Number : 840125, New York
RECRUITING
Mt. Sinai School of Medicine- Site Number : 840005, New York
RECRUITING
Investigational Site Number : 2140001, Santo Domingo
RECRUITING
Investigational Site Number : 764003, Bangkok
RECRUITING
Investigational Site Number : 152321, Taipei
RECRUITING
New York Medical College- Site Number : 840039, Valhalla
RECRUITING
Investigational Site Number : 764004, Bangkok
RECRUITING
Investigational Site Number : 688001, Belgrade
RECRUITING
Investigational Site Number : 688002, Belgrade
RECRUITING
Investigational Site Number : 688003, Belgrade
RECRUITING
Investigational Site Number : 688005, Belgrade
RECRUITING
Northwell Health- Site Number : 840102, Manhasset
RECRUITING
Investigational Site Number : 300002, Athens
RECRUITING
Investigational Site Number : 9829, Cairo
RECRUITING
Investigational Site Number : 150809, Prague
RECRUITING
State University of New York- Site Number : 840052, Syracuse
TERMINATED
Investigational Site Number : 250011, Marseille
RECRUITING
Investigational Site Number : 151686, Berlin
COMPLETED
Investigational Site Number : 250002, Caen
RECRUITING
University of Rochester Medical Center SOM- Site Number : 840105, Rochester
COMPLETED
Investigational Site Number : 154146, A Coruña
RECRUITING
University of Pittsburgh- Site Number : 840023, Pittsburgh
RECRUITING
Investigational Site Number : 380006, Genova
RECRUITING
Penn State Health Milton South Hershey Medical Center- Site Number : 840126, Hershey
RECRUITING
Investigational Site Number : 688004, Niš
RECRUITING
Children's Hospital of Philadelphia HUP Medical Genetics- Site Number : 840089, Philadelphia
RECRUITING
Children's National Medical Center- Site Number : 840067, Washington D.C.
RECRUITING
Investigational Site Number : 151369, Hamburg
RECRUITING
Investigational Site Number : 380004, Milan
COMPLETED
Investigational Site Number : 151368, Hamburg
ACTIVE_NOT_RECRUITING
Investigational Site Number : 151726, Malmo
RECRUITING
Investigational Site Number : 380002, Monza (MB)
RECRUITING
Investigational Site Number : 682004, Mecca
RECRUITING
O&O Alpan, LLC- Site Number : 840025, Fairfax
COMPLETED
University of Virginia School of Medicine-Pediatrics- Site Number : 840078, Charlottesville
RECRUITING
Investigational Site Number : 151534, New Taipei City
COMPLETED
Children's Hospital of the Kings Daughters- Site Number : 840072, Norfolk
COMPLETED
Investigational Site Number : 250004, Besançon
RECRUITING
Investigational Site Number : 300003, Pátrai
RECRUITING
Duke University Medical Center Genetics Dept- Site Number : 840037, Durham
RECRUITING
Investigational Site Number : 154163, Madrid
RECRUITING
Investigational Site Number : 154236, Madrid
RECRUITING
Investigational Site Number : 151524, Madrid
TERMINATED
Investigational Site Number : 153251, Madrid
RECRUITING
Investigational Site Number : 154199, Madrid
RECRUITING
Investigational Site Number : 154160, Madrid
RECRUITING
Carolinas Medical Center Hospital- Site Number : 840065, Charlotte
RECRUITING
Investigational Site Number : 154119, Alcorcón
RECRUITING
Investigational Site Number : 250005, Brest
RECRUITING
Greenwood Genetcs- Site Number : 840055, Greenville
RECRUITING
Emory University School of Medicine- Human Genetics- Site Number : 840060, Decatur
COMPLETED
Investigational Site Number : 250017, Toulouse
RECRUITING
University of Florida Pediatrics Genetics- Site Number : 840121, Jacksonville
COMPLETED
The Atwal Clinic- Site Number : 840112, Jacksonville
RECRUITING
Investigational Site Number : 250008, Bordeaux
RECRUITING
University Hematology Oncology- Site Number : 840075, Coral Springs
RECRUITING
Investigational Site Number : 380001, Udine
RECRUITING
University Of Miami SOM- Site Number : 840006, Miami
RECRUITING
University of Florida-Genetics- Site Number : 840096, Tampa
COMPLETED
Pediatric Endocrine Associates- Site Number : 840017, Tampa
RECRUITING
Investigational Site Number : 2500013, Montpellier
RECRUITING
Investigational Site Number : 380003, Padua
RECRUITING
Investigational Site Number : 250012, Rennes
RECRUITING
Investigational Site Number : 154150, Giessen
RECRUITING
Investigational Site Number : 153213, Vigo
RECRUITING
Investigational Site Number : 682002, Al Mubarraz
RECRUITING
Investigational Site Number : 250016, Tours
RECRUITING
Vanderbilt University Hospital-Pediatrics- Site Number : 840049, Nashville
RECRUITING
Investigational Site Number : 764005, Khon Kaen
COMPLETED
University of Louisville- Genetics- Site Number : 840030, Louisville
RECRUITING
Investigational Site Number : 150783, Düsseldorf
RECRUITING
Investigational Site Number : 153215, Seville
RECRUITING
Investigational Site Number : 153219, Seville
RECRUITING
Investigational Site Number : 380005, Modena
RECRUITING
LSD Data Registry Site LLC- Site Number : 840094, Dublin
RECRUITING
Investigational Site Number : 250006, Nantes
RECRUITING
University Hospitals Cleveland Medical Center- Site Number : 840119, Cleveland
RECRUITING
Cleveland Clinic Foundation Pediatrics- Site Number : 840048, Cleveland
RECRUITING
Investigational Site Number : 154205, Valencia
COMPLETED
Investigational Site Number : 150432, Oberhausen
RECRUITING
Indianapolis University School of Medicine- Site Number : 840027, Indianapolis
RECRUITING
University of Michigan Pediatrics- Site Number : 840107, Ann Arbor
RECRUITING
Children's Hospital of Michigan- Site Number : 840066, Detroit
COMPLETED
Spectrum for Health- Site Number : 840019, Grand Rapids
COMPLETED
Infusion Associates- Site Number : 840050, Grand Rapids
RECRUITING
Investigational Site Number : 154238, Zaragoza
RECRUITING
Investigational Site Number : 153216, Zaragoza
COMPLETED
Investigational Site Number : 380009, Florence
RECRUITING
Investigational Site Number : 458001, Jalan Pahang
TERMINATED
Investigational Site Number : 154208, Yangsan
RECRUITING
University of Iowa- Site Number : 840032, Iowa City
RECRUITING
Children's Hospital of Wisconsin-Pediatrics- Site Number : 840054, Milwaukee
RECRUITING
Investigational Site Number : 150031, Mainz
RECRUITING
Children's Health Care- Site Number : 840114, Minneapolis
RECRUITING
Children's Hospital and Clinics of Minnesota- Site Number : 840046, Minneapolis
RECRUITING
University of Minnesota Medical Center Pediatrics- Site Number : 840076, Minneapolis
RECRUITING
Investigational Site Number : 458002, Kuala Lumpur
RECRUITING
Investigational Site Number : 154092, Norrköping
RECRUITING
Ann and Robert Lurie Children's Hospital- Site Number : 840011, Chicago
RECRUITING
Ann and Robert Lurie Children's Hospital- Site Number : 840013, Chicago
RECRUITING
Rush University Medical Center Genetics- Site Number : 840079, Chicago
RECRUITING
Washington University of St. Louis- Site Number : 840100, St Louis
COMPLETED
Children's Mercy Hospital- Pediatrics- Site Number : 840063, Kansas City
RECRUITING
University of Missouri Health System Department of Genetics- Site Number : 840031, Columibia
RECRUITING
Investigational Site Number : 250018, Strasbourg
RECRUITING
University of Nebraska Medical Center- Pediatrics- Site Number : 840084, Omaha
COMPLETED
Investigational Site Number : 250009, Lyon
RECRUITING
Investigational Site Number : 250014, Bron
COMPLETED
Tulane University Medical Center- Site Number : 840001, New Orleans
RECRUITING
Arkansas Childrens Hospital- Site Number : 840109, Little Rock
RECRUITING
University of Arkansas for Medical Sciences- Site Number : 840113, Little Rock
TERMINATED
Investigational Site Number : 250007, Paris
RECRUITING
Investigational Site Number : 250010, Paris
RECRUITING
Baylor Research Center- Site Number : 840058, Dallas
RECRUITING
Cook Children's Health Care System- Site Number : 840024, Fort Worth
RECRUITING
University of Colorado at Denver Genetics- Site Number : 840068, Aurora
COMPLETED
Investigational Site Number : 703001, Bratislava
RECRUITING
University of Utah Department of Medical Genetics- Site Number : 840043, Salt Lake City
RECRUITING
Phoenix Children's Hospital- Site Number : 840003, Phoenix
RECRUITING
University of Arizona- Site Number : 840015, Tucson
RECRUITING
Children's Specialty Center of Nevada- Site Number : 840008, Las Vegas
RECRUITING
Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
COMPLETED
USC Health Sciences Center Dept of Genetics- Site Number : 840082, Los Angeles
RECRUITING
Tower Hematology/Oncology Medical Group- Site Number : 840056, Beverly Hills
COMPLETED
University of California at San Diego- Site Number : 840007, San Diego
RECRUITING
Investigational Site Number : 250001, Clichy
RECRUITING
Investigational Site Number : 250003, Garches
RECRUITING
University of California at Irvine- Site Number : 840036, Irvine
RECRUITING
Children's Hospital of Orange County- Site Number : 840074, Orange
RECRUITING
Stanford Unviersity MC Dept of Genetics- Site Number : 840022, Palo Alto
RECRUITING
Investigational Site Number : 380008, Catania
RECRUITING
UC Davis MIND Institute- Site Number : 840010, Sacramento
COMPLETED
Kaiser Permanente Hospital- Site Number : 840042, Sacramento
RECRUITING
Oregon Health and Science University- Site Number : 840080, Portland
RECRUITING
Seattle Children's Hospital- Site Number : 840028, Seattle
RECRUITING
University Of Washington Medical Center- Site Number : 840059, Seattle
RECRUITING
Multicare Health System ¿ Mary Bridge Childrens Hospital- Site Number : 840115, Tacoma
TERMINATED
Investigational Site Number : 151787, Beijing
RECRUITING
Investigational Site Number : 1560001, Beijing
RECRUITING
Investigational Site Number : 422001, Beirut
TERMINATED
Investigational Site Number : 152356, Shanghai
RECRUITING
Investigational Site Number : 702001, Singapore
COMPLETED
Investigational Site Number : 356004, Jaipur
TERMINATED
Investigational Site Number : 152358, Hangzhou
RECRUITING
Investigational Site Number : 356003, Ahmedabad
RECRUITING
Investigational Site Number : 642001, Cluj-Napoca
RECRUITING
Investigational Site Number : 356005, Mumbai
COMPLETED
Investigational Site Number : 151188, Cluj-Napoca
RECRUITING
Investigational Site Number : 642002, Cluj-Napoca
RECRUITING
Investigational Site Number : 3560006, Secunderabad
TERMINATED
Investigational Site Number : 152357, Guangzhou
RECRUITING
Investigational Site Number : 1560002, Guangzhou
RECRUITING
Investigational Site Number : 356002, Vellore
RECRUITING
Investigational Site Number : 704002, Ho Chi Minh City
RECRUITING
Investigational Site Number : 356001, Kolkata
RECRUITING
University of California at San Francisco- Site Number : 840051, San Francisco
COMPLETED
John Hopkins- Site Number : 840044, Baltimore
TERMINATED
Cooper Health Center- Site Number : 840098, Camden
RECRUITING
Site Number : 840026, New York
RECRUITING
Children's Hospital of Philadelphia- Site Number : 840034, Philadelphia
RECRUITING
Investigational Site Number : 151164, Sofia
TERMINATED
Investigational Site Number : 156003, Beijing
TERMINATED
Investigational Site Number : 152359, Hangzhou
TERMINATED
Investigational Site Number : 150899, Shanghai
RECRUITING
Investigational Site Number : 170004, Bogotá
RECRUITING
Investigational Site Number : 818007, Al Mansurah
RECRUITING
Investigational Site Number : 5748, Alexandria
RECRUITING
Investigational Site Number : 9889, Ash Sharqia
RECRUITING
Investigational Site Number : 9888, Asyut
RECRUITING
Investigational Site Number : 8345, Cairo
RECRUITING
Investigational Site Number : 9830, Cairo
RECRUITING
Investigational Site Number : 300004, Athens
RECRUITING
Investigational Site Number : 344001, Kowloon
RECRUITING
Investigational Site Number : 360001, Jakarta
RECRUITING
Investigational Site Number : 3760003, Haifa
RECRUITING
Investigational Site Number : 3760001, Jerusalem
RECRUITING
Investigational Site Number : 3760002, Petah Tikva
RECRUITING
Investigational Site Number : 380011, Monza
RECRUITING
Investigational Site Number : 380010, Napoli
COMPLETED
Investigational Site Number : 154225, Kuwait City
RECRUITING
Investigational Site Number : 4220004, Beirut
COMPLETED
Investigational Site Number : 150149, Amsterdam
TERMINATED
Investigational Site Number : 151171, Amsterdam
RECRUITING
Investigational Site Number : 154264, Karachi
RECRUITING
Investigational Site Number : 154266, Lahore
RECRUITING
Investigational Site Number : 604001, Arequipa
RECRUITING
Investigational Site Number : 620003, Coimbra
RECRUITING
Investigational Site Number : 643001, Moscow
RECRUITING
Investigational Site Number : 643002, sait-Petersburg
COMPLETED
Investigational Site Number : 682003, Jeddah
RECRUITING
Investigational Site Number : 710-003, Johannesburg
RECRUITING
Investigational Site Number : 153191, Daejeon
RECRUITING
Investigational Site Number : 153212, Seoul
RECRUITING
Investigational Site Number : 153222, Seoul
RECRUITING
Investigational Site Number : 154093, Chiayi City
RECRUITING
Investigational Site Number : 152152, Hualien City
RECRUITING
Investigational Site Number : 151500, Putz City, Chia-yi
RECRUITING
Investigational Site Number : 764001, Bangkok
RECRUITING
Investigational Site Number : 792001, Ankara
RECRUITING
Investigational Site Number : 792002, Ankara
RECRUITING
Investigational Site Number : 792004, Istanbul
RECRUITING
Investigational Site Number : 792007, Izmir
RECRUITING
Investigational Site Number : 792003, Malatya
RECRUITING
Investigational Site Number : 7840001, Dubai
RECRUITING
Investigational Site Number : 154212, Hanoi
RECRUITING
Yale - Site Number : 840047, New Haven
RECRUITING
Maine Medical Center Pediatrics- Site Number : 840064, Portland
RECRUITING
Massachusetts General Hospital-Genetics- Site Number : 840062, Boston
RECRUITING
Joseph M. Sanzari Children's Hospital- Site Number : 840101, Hackensack
RECRUITING
Atlantic Health System- Site Number : 840099, Morristown
RECRUITING
St. Peter's University Hospital- Site Number : 840016, New Brunswick
RECRUITING
St. Joseph's Children's Hospital- Site Number : 840057, Paterson
RECRUITING
Metropolitan Hospital Center- Site Number : 840110, New York
RECRUITING
Nationwide Children's Hospital- Site Number : 840091, Columbus
COMPLETED
Rhode Island Hospital Genetics- Site Number : 840053, Providence
RECRUITING
Investigational Site Number : 032011, Córdoba
RECRUITING
Hospital das Clínicas da Universidade Federal do Paraná - HCUFPR- Site Number : 076010, Curitiba
RECRUITING
Hospital de Clinicas de Porto Alegre- Site Number : 076007, Porto Alegre
RECRUITING
Hospital e Maternidade Celso Pierro - PUC-Campinas- Site Number : 076012, Campinas
RECRUITING
Hospital das Clinicas da Faculdade de Medicina de Ribeirao Preto- Site Number : 076001, Ribeirão Preto
RECRUITING
Faculdade De Medicina - Unicamp- Site Number : 076005, Campinas
RECRUITING
HEMORIO- Site Number : 076006, Rio de Janeiro
RECRUITING
Instituto de Genética e Erros Inatos do Metabolismo- Site Number : 076002, São Paulo
RECRUITING
Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo- Site Number : 076008, São Paulo
RECRUITING
Investigational Site Number : 124014, Calgary
RECRUITING
Investigational Site Number : 124002, Edmonton
RECRUITING
Investigational Site Number : 124010, Vancouver
COMPLETED
Investigational Site Number : 124011, Vancouver
RECRUITING
Investigational Site Number : 124019, Winnipeg
RECRUITING
Investigational Site Number : 124022, Moncton
RECRUITING
Investigational Site Number : 124024, Kingston
TERMINATED
Investigational Site Number : 124005, Kingston
RECRUITING
Investigational Site Number : 124021, London
RECRUITING
Investigational Site Number : 124006, Toronto
RECRUITING
Investigational Site Number : 124013, Toronto
RECRUITING
Investigational Site Number : 124001, Sherbrooke
RECRUITING
Investigational Site Number : 300001, Thessaloniki
RECRUITING
Investigational Site Number : 3480006, Budapest
RECRUITING
Investigational Site Number : 380007, Rome
RECRUITING
Investigational Site Number : 380014, Sassari
COMPLETED
Investigational Site Number : 153205, Abeno-ku
COMPLETED
Investigational Site Number : 153203, Yonago-shi
RECRUITING
Investigational Site Number : 153217, Chiba
RECRUITING
Investigational Site Number : 153204, Tokyo
RECRUITING
Investigational Site Number : 154237, Vilnius
RECRUITING
Investigational Site Number : 604002, Callao
RECRUITING
Investigational Site Number : 150575, Warsaw
RECRUITING
Investigational Site Number : 620004, Lisbon
RECRUITING
Investigational Site Number : 620009, Ponta Delgada
RECRUITING
Investigational Site Number : 153180, Seoul
RECRUITING
Investigational Site Number : 153196, Seoul
RECRUITING
Investigational Site Number : 151149, Seoul
RECRUITING
Investigational Site Number : 153237, Barcelona
RECRUITING
Investigational Site Number : 154147, Barcelona
RECRUITING
Investigational Site Number : 154145, Sabadell
COMPLETED
Investigational Site Number : 154095, Borås
RECRUITING
Investigational Site Number : 151181, Taichung
RECRUITING
Investigational Site Number : 792006, Adana
RECRUITING
Investigational Site Number : 792005, Ankara
RECRUITING
Investigational Site Number : 151340, Cambridge
RECRUITING
Investigational Site Number : 152287, Birmingham
RECRUITING
Investigational Site Number : 151646, London
RECRUITING
Investigational Site Number : 150303, London
RECRUITING
Investigational Site Number : 152361, Salford
RECRUITING
Investigational Site Number : 154240, Birmingham
RECRUITING
Investigational Site Number : 151123, London
RECRUITING
Investigational Site Number : 150455, Manchester
Genzyme, a Sanofi Company
INDUSTRY