Phase 3/4 Study of a Recombinant Protein-Free Factor VIII (rAHF-PFM): Comparison of Continuous Infusion Versus Intermittent Bolus Infusion in Hemophilia A Subjects Undergoing Major Orthopedic Surgery

PHASE4CompletedINTERVENTIONAL
Enrollment

85

Participants

Timeline

Start Date

May 29, 2006

Primary Completion Date

October 1, 2015

Study Completion Date

December 9, 2015

Conditions
Hemophilia A
Interventions
DRUG

Recombinant Protein-Free Factor VIII (rAHF-PFM)

"An initial loading dose will be administered intravenously over a period \<= 5 minutes (maximum of infusion rate of 10 mL/minute) within 60 minutes prior to surgery dose in order to maintain a minimum target FVIII level of at least 80% of normal.~CI will start prior to surgery as soon as the loading dose has been administered, at a rate calculated according to a formula provided by the sponsor.~All study product must be administered with a syringe pump running at an infusion rate according to the dosing regimen, but always \>= 0.4 mL/h."

DRUG

Recombinant Protein-Free Factor VIII (rAHF-PFM)

The treatment schedule for intermittent BI of rAHF-PFM will begin with the administration of the loading dose according to the dose recommendations provided by the sponsor. If required by the hemostatic challenge, additional boluses may be administered after a blood sample for FVIII determination has been drawn. All infusions of rAHF PFM will be given over a period \<= 5 minutes (maximum infusion rate, 10 mL/min).

Trial Locations (36)

1090

University Hospital for Internal Medicine I (Hematology/Hemostaseology), Vienna

1100

AMC Medical Research BV, Department of Vascular Medicine, Amsterdam

1134

State Health Centre, National Hemophilia Centre, Budapest

1200

Cliniques Universitaires St. Luc, Haematology Department, Brussels

3000

University Hospital Gasthuisberg, Leuven

4012

University of Debrecen, 2nd Dept of Internal Medicine, Debrecen

6229

Academic Hospital Maastricht, Maastricht

7624

PTE ÁOK I. Internal Medical Clinic, Dept of Hematology, Pécs

9713

University Medical Centre Groningen, Groningen

11156

National Blood Transfusion Institute, Bucharest

17033

Penn State Milton S. Hershey Medical Center, Hershey

20057

Georgetown University, Washington D.C.

20122

"Centro Emofilia e Trombosi Angelo Bianchi Bonomi", Milan

20502

University Hospital MAS, Department for Coagulation Disorders, Malmo

21205

Johns Hopkins Medical Institutions, Baltimore

40202

James Graham Brown Cancer Center, Louisville

46990

Hospital Universitario La Fe, Valencia

60612

Rush Presbyterian St. Lukes, Chicago

69437

Hôpital Edouard Herriot, Lyon

77030

The University of Texas Health Science Center at Houston Medical School, Houston

80129

Department of Clinical & Experimental Medecine, AOU Federico II, Naples

90007

Los Angeles Orthopaedic Hospital, Los Angeles

125167

Hematology Research Center under Russian Academy of Medical Sciences, Department of Reconstructive Orthopedic Surgery for Hemophilia Patients, Moscow

191024

Russian Research Institute of Hematology and Transfusiology, Department of Surgical Hematology and Angiology, Saint Petersburg

610027

Regional Hemophilia Center, Kirov

70112-2699

Tulane University, New Orleans

02115

Brigham and Women´s Hospital, Boston

44106-6010

University Hospitals of Cleveland, Cleveland

0027

Rikshospitalet, Oslo

30-224

Krakowskie Centrum Rehabilitacji, Krakow

02-776

Instytut Hematologii i Transfuzjologii, Klinika Zaburzeń Hemostazy i Chorób Wewnętrznych, Warsaw

3040-316

Centro Hospitalar de Coimbra, Coimbra

4900-001

Hospital Santo António, Porto

022328

"Fundeni Clinical Institute, Clinical Laboratory St. Berceanu Hematology and Bone Marrow Transplantation Department", Bucharest

"Louis Turcanu Emergency Clinical Children´s Hospital, 3rd Pediatrics Department, Hemophilia Center", Timișoara

08035

Hospital Vall d´Hebron, Servei d´Hemofilia, Barcelona

All Listed Sponsors
collaborator

Baxalta Innovations GmbH, now part of Shire

INDUSTRY

lead

Baxalta now part of Shire

INDUSTRY

NCT00357656 - Phase 3/4 Study of a Recombinant Protein-Free Factor VIII (rAHF-PFM): Comparison of Continuous Infusion Versus Intermittent Bolus Infusion in Hemophilia A Subjects Undergoing Major Orthopedic Surgery | Biotech Hunter | Biotech Hunter