3
Participants
Start Date
August 31, 2004
Primary Completion Date
October 31, 2007
Study Completion Date
October 31, 2007
Retrovirus Construct
This study will use an experimental gene transfer procedure performed in a laboratory to insert a new FA gene into the participant's bone marrow cells. The gene-corrected bone marrow cells will then be re-infused into the participant and participants will be observed for successful gene transfer
Cincinnati Children's Hospital Medical Center, Cincinnati
National Heart, Lung, and Blood Institute (NHLBI)
NIH
Children's Hospital Medical Center, Cincinnati
OTHER
Boston Children's Hospital
OTHER