39
Participants
Start Date
May 31, 2006
Primary Completion Date
July 31, 2011
Study Completion Date
July 31, 2011
University of Rochester School of Medicine, Rochester
University of Kansas Medical Center, Kansas City
Reed Neurological Research Center, UCLA, Los Angeles
Brigham & Women's Hospital, Boston
London Health Sciences Centre, London
Institute of Neurology, Center for Neuromuscular Disease, Queen Square
Office of Rare Diseases (ORD)
NIH
Rare Diseases Clinical Research Network
NETWORK
University of California, Los Angeles
OTHER