A Study of rhGAA in Patients With Late-Onset Pompe Disease

PHASE2CompletedINTERVENTIONAL
Enrollment

5

Participants

Timeline

Start Date

February 28, 2005

Primary Completion Date

July 31, 2006

Study Completion Date

November 30, 2006

Conditions
Pompe Disease (Late-onset)Glycogen Storage Disease Type II (GSD-II)Acid Maltase Deficiency DiseaseGlycogenosis 2
Interventions
BIOLOGICAL

Myozyme

20 mg/kg qow

Trial Locations (1)

3015

Sophia Kinderziekenhuis, Erasmus MC, Rotterdam

All Listed Sponsors
lead

Genzyme, a Sanofi Company

INDUSTRY

NCT00250939 - A Study of rhGAA in Patients With Late-Onset Pompe Disease | Biotech Hunter | Biotech Hunter