Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)

CompletedOBSERVATIONAL
Enrollment

237

Participants

Timeline

Start Date

July 31, 2005

Primary Completion Date

May 1, 2020

Study Completion Date

May 1, 2020

Conditions
Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)
Trial Locations (50)

4029

Royal Children's Hospital, Brisbane, Brisbane

5006

Women and Children's Hospital, Adelaide

6008

Princess Margaret Hospital for Children, Subiaco

6041

Institute of Pathology and Genetics, Metabolic Unit, Charleroi

10016

New York University, New York

13353

Charité-Universitätsmedizin Berlin, Berlin

15224

Children's Hospital of Pittsburgh, Pittsburgh

19104

Children's Hospital of Philadelphia, Philadelphia

20052

"Università Milano Bicocca, Resp. Centro Fondazione Mariani", Monza

20246

Universitätsklinikum Hamburg Eppendorf, Hamburg

21287

Johns Hopkins Univeristy School of Medicine, Baltimore

23507

Children's Hospital of the King's Daughters, Norfolk

28203

Carolinas Medical Center, Charlotte

28803

Fullerton Genetic Center, Asheville

30033

Emory University, Decatur

30173

Oberarzt Pädiatrie, Hanover

35128

Department of Woman's and Child's Health, Padua

46202

Indiana University School of Medicine, Indianapolis

55131

Universitätsmedizin, Mainz

55404

Children's Health Care, Minneapolis

55455

University of Minnesota - Fairview University Medical Center, Minneapolis

57117

Sioux Valey Children's Speciality Clinics, Sioux Falls

60611

Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago

64108

Children's Mercy Hospital, Kansas City

69677

Hôpital Femme Mère Enfant, Bron

70112

Tulane University Medical Center, New Orleans

70808

Baton Rouge Clinic, Baton Rouge

79106

Universitatsklinikum Freiburg, Klinik II, Kammin

84132

University of Utah Medical Center, Salt Lake City

90027

Children's Hospital of Los Angeles, Los Angeles

92697

University of California, Irvine, Irvine

94609

Children's Hospital and Research Center Oakland, Oakland

95123

Azienda Ospedaliero Universitaria, Cibali

97239

Oregon Health and Science University, Portland

98105

Seattle Children's Hospital, Seattle

07503

St. Joseph's Healthcare, Paterson

NSW2145

Westmead Hospital, Wentworthville

Unknown

Royal Children's Hospital, Parkville

Hopital Necker - Enfants Malades, Paris

MidWestern Regional Hospital, Limerick

Astrid Lindgrens Children's Hospital, Stockholm

A-8036

LKH-Universitätsklinik Graz, Kinderklinik, Graz

LT-08661

Vilnius University Hospital, Santariskiu Klinikos, Vilnius

3015 GE

Rotterdam University Hospital - Sophia's Children's Hospital, Rotterdam

4200-319

Hospital de Sao Joao, Unidae de Doencas Metabolicas, Porto

B29 6JD

Queen Elizabeth Hospital, University Hospitals Birmingham NHS, Birmingham

B4 6NH

Birmingham Children's Hospital, Steelhouse, Birmingham

WC1N 3JH

Great Ormond Street Hospital For Children, NHS Foundation Trust, London

M13 9WL

St Mary's Hospital, Willink Biochemical Genetics Unit, Manchester

M6 8HD

Salford Royal Hospital NHS Trust, Salford

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY