Study of rhASB in Patients With Mucopolysaccharidosis VI

PHASE3CompletedINTERVENTIONAL
Enrollment

39

Participants

Timeline

Start Date

February 29, 2004

Primary Completion Date

October 31, 2006

Study Completion Date

October 31, 2006

Conditions
Mucopolysaccharidosis VI
Interventions
DRUG

N-acetylgalactosamine 4-sulfatase

DRUG

Placebo/rhASB

Trial Locations (1)

94949

BioMarin Pharmaceutical Inc., Novato

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY