A Survival Study in Patients With High Risk Myelodysplastic Syndromes Comparing Azacitidine Versus Conventional Care

PHASE3CompletedINTERVENTIONAL
Enrollment

358

Participants

Timeline

Start Date

November 1, 2003

Primary Completion Date

July 1, 2007

Study Completion Date

July 1, 2007

Conditions
Myelodysplastic Syndromes
Interventions
DRUG

Azacitidine

Azacitidine was injected subcutaneously (SC) at an initial dose of 75mg/m\^2/day for 7 days. The 7-day dosing was repeated every 28 days with dose adjustment based on predefined hematology and renal laboratory results. Number of cycles: Azacitidine treatment was to be continued until the end of the study unless treatment was discontinued due to unacceptable toxicity, relapse after complete or partial response, transformation to AML or disease progression.

OTHER

Physician Choice

"Physician Choice was one of three options:~* Best supportive care (BSC) alone,~* Low-dose cytarabine subcutaneously for 14 days every 28 to 42 days, or~* Standard chemotherapy administered for induction as a continuous intravenous infusion of cytarabine over 7 days plus an anthracycline (daunorubicin, idarubicin, or mitoxantrone) on Days 1, 2, and 3; and, for those eligible, 1 or 2 consolidation cycles administered as continuous intravenous infusions of cytarabine for 3 to 7 days with the same anthracycline that was used at induction on Days 1 and 2 (each cycle between 28 to 70 days from the start of the previous cycle).~All three options included best supportive care"

Trial Locations (108)

144

"Instituto Nazionale Tumori Regina Elena", Roma

1135

Orszagos Gyogyintezeti Kozpont, Budapest

1307

Universitatsklinikum Carl Gustav Carus, Dresden

1756

National Centre of Hematology and Transfusiology, Sofia, Sofia

2065

Royal North Shore Hospital, St Leonards

2170

Liverpool Hospital, Liverpool

2298

The Newcastle Mater Miseriecordiae Hospital, Warratah

3002

Peter MacCallum Cancer Institute, East Melbourne

3010

"Multiprofile Hospital for Active Treatment (MHAT), St. Marina Clinic of Hematology", Varna

3050

Royal Melbourne Hospital, Melbourne

3181

The Alfred Hospital, Melbourne

4002

"MHAT St George Clinic of Hematology, Plovdiv", Plovdiv

4004

III-rd Internal Department, District Dispensary for Oncology diseases with stationary(DDOncDIU), Plovdiv

4029

Royal Brisbane Hospital, Hersten

4102

Princess Alexandra Hospital, Woolloongabba

5000

Royal Adelaide Hospital, Adelaide

5800

First Clinical Base - Clinic of Hematology, MHAT - Pleven, Pleven

6701

University of Szeged, 2nd Department of Internal Medicine, Szeged

6847

The Royal Perth Hospital, Perth

7100

Universita Degli Studi Di Sassari, Sassari

7624

University of Pecs, 1st Dept of Internal Medicine, Pécs

9010

"University Multiprofile Hospital for Active Treatment Sveta Marina", Varna

9113

Klinikum Chemnitz gGmbH, Chemnitz

11527

District General Hospital of Athens, Athens

General Hospital of Chest Disease, Athens

12462

University Hospital-Attikon, Haidari

13009

Institute Paoli Calmettes, Marseille

14186

Huddinge University Hospital, Stockholm

15224

Western Pennsylvania Cancer Institute, Pittsburgh

20081

Samodzielny Publiczny Szpital Kliniczny, Lublin

20133

Instituto Nazionale Dei Tumori, Milan

22185

Lund Universtiy Hospital, Lund

24071

Hospital de Leon, León

26500

University General Hospital of Patra Rio, Pátrai

28006

Hospital Universitario De La Princesa, Madrid

28034

Hospital Ramon Y Cajal, Madrid

28046

Hospital La Paz, Madrid, Madrid

28048

Hospital Clinico San Carlos, Madrid

31059

Chu Purpan, Toulouse

35294

University of Alabama School of Medicine, Birmingham

37007

Hospital Universitario Del Salamanca, Salamanca

37075

Gerorg-August-Universitat Gottingen, Göttingen

40138

Policlinico S. Orsola-Malpighi, Bologna

40225

Heinrich-Heine University Dusseldorf, Düsseldorf

41100

Centro Oncologico Modenese, Modena

44093

Chu De Nantes, Nantes

44106

Case Western Reserve University, Cleveland

45147

University Essen, Essen

45500

University General Hospital of Ioannina, Ioannina

46009

Hospital Universitario La Fe, Valencia

46202

Indiana University Cancer Center, Indianapolis

47166

St Johannes Hospital, Duisburg

49033

Chu D'Angers, Angers

50139

Universita di Firenze, Florence

53105

Universitatsklinikum Bonn, Bonn

53226

Froedtert Memorial Lutheran Hospital, Milwaukee

59037

Che De Lille, Lille

63110

Washington University School of Medicine, St Louis

69437

Hospital Edouard Herriot, Lyon

71013

Ospedale Casa Sollievo Della Sofferenza - Irrc, San Giovanni Rotondo

71110

University General Hospital of Heraklio Voutes, Heraklio

75010

Hospital Saint Louis, Paris

75679

Hopital Cochin, Paris

76038

Centre Henri Becquerel, Rouen

89070

Universitatsklinikum Ulm, Ulm

92110

Hopital Beaujon, Clichy

97201

Oregon Cancer Center, Portland

105299

Burdenko Central Military Clinical Hospital, Moscow

115487

Blokhin Cancer Research Center, Moscow

125167

Scientific Haematology Center, Moscow, Moscow

193024

Institute of Haematology & Blood Transfusion, Saint Petersburg

197022

Pavlov State Medical University, Saint Petersburg

197089

Pavlov State Medical University, Saint Petersburg

197110

City Hospital #31, Saint Petersburg

10029-6574

Mount Sinai Medical Center, New York

639 00

Fakultni nemocnice Brno, Jihlavska

500 05

Fakultni nemocnice Hradec Kralove, Sokolska

775 20

Fakultni Nemocnice Olomouc, Olomouc

2 128 08

Vseobecna Fakultni Nemocnice, Prague

2 128 20

Uslav Hematologie a Krevni Transfuze, Prague

D-12203

Universitatsklinikum Benjamin Franklin, Hindenburgdamm

D-20099

Allgemeines Krankenhaus St. Georg, Hamburg

D-20246

Universitatsklinikum Hambur-Eppendorf, Hamburg

D-24116

Universitatsklinikum Kiel II, Kiel

I-16132

Ospedale San Martino, Genova

00144

Ospedale San Eugenio, Roma

00168

Policlinico Gemelli, Roma

1081 HV

VU University Medical Center Amsterdam, Amsterdam

Unknown

Univ Hospital St. Radboud, Nijmejen

Hospital Universitario Germans Trias I Pujol, Barcelona

Kings College Hospital NHS Trust, London

80-952

Samodzielny Publiczny Szpital Kliniczny Nr 1, Gdansk

93-510

Wojewodzki Szpital Specjalistyczny, Lodz

00-909

Wojskowy Instytut Medyczny, Warsaw

02-097

Samodzelny Publiczny Centralny Szpital Kliniczny, Warsaw

50-367

Samodzielny Publiczny Szpital Kliniczny Nr 1, Wroclaw

08025

Hospital Santa Creu I Sant Pau, Barcelona

08036

Hospital Clinic, Barcelona

07198

Hospital Son Llatzer, Palma de Mallorca

S-413 45

Sahlgrenska University Hospital, Gothenburg

S-205 02

University Hospital MAS, Malmo

S-751 85

Uppsala University Hospital, Uppsala

BH7 7DW

Royal Bournemouth General Hospital, Bournemouth

EC1A 7BE

St. Bartholomew's Hospital, London

M20 4BX

Christie Hospital, Manchester

NR4 7UY

Norfolk and Norwich University Hospital, Norwich

OX3 9DU

John Radcliffe Hospital, Oxford

TR1 3LJ

Royal Cornwall Hospital, Truro

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Celgene

INDUSTRY

NCT00071799 - A Survival Study in Patients With High Risk Myelodysplastic Syndromes Comparing Azacitidine Versus Conventional Care | Biotech Hunter | Biotech Hunter