Study of Recombinant Human N-acetylgalactosamine 4-sulfatase (rhASB) in Patients With MPS VI

PHASE3CompletedINTERVENTIONAL
Enrollment

39

Participants

Timeline

Start Date

September 30, 2003

Study Completion Date

March 31, 2004

Conditions
Mucopolysaccharidosis VI
Interventions
DRUG

Placebo

DRUG

N-acetylgalactosamine 4-sulfatase

Trial Locations (1)

94949

BioMarin Pharmaceutical Inc., Novato

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY