NCT00007020View on ClinicalTrials.gov

Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

PHASE3CompletedINTERVENTIONAL
Enrollment

85

Participants

Timeline

Start Date

January 31, 1992

Primary Completion Date

December 31, 2009

Study Completion Date

December 31, 2009

Conditions
Infantile Refsum's DiseaseZellweger SyndromeAdrenoleukodystrophyPeroxisomal DisordersCholestasis
Interventions
DRUG

Cholic Acids

10-15 mg/kg body weight/day taken orally.

Trial Locations (1)

45229-3039

Cincinnati Children's Hospital Medical Center, Cincinnati

Sponsors
All Listed Sponsors
collaborator

Children's Hospital Medical Center, Cincinnati

OTHER

lead

Mirum Pharmaceuticals, Inc.

INDUSTRY