Phase I Study of Ex Vivo Liver-Directed Gene Therapy for Familial Hypercholesterolemia

PHASE1CompletedINTERVENTIONAL
Enrollment

5

Participants

Timeline

Start Date

June 30, 1992

Conditions
Familial Hypercholesterolemia
Interventions
PROCEDURE

gene therapy

All Listed Sponsors
collaborator

University of Pennsylvania

OTHER

lead

National Center for Research Resources (NCRR)

NIH

NCT00004809 - Phase I Study of Ex Vivo Liver-Directed Gene Therapy for Familial Hypercholesterolemia | Biotech Hunter | Biotech Hunter