Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)
PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment
2
Participants
Timeline
Start Date
October 31, 1996
Conditions
Mucopolysaccharidosis II
Interventions
GENETIC
lymphocyte gene therapy
Trial Locations (1)
55455
University of Minnesota Medical School, Minneapolis
All Listed Sponsors
collaborator
University of Minnesota
OTHER
lead
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
NIH
NCT00004454 - Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome) | Biotech Hunter | Biotech Hunter