Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency

PHASE1TerminatedINTERVENTIONAL
Timeline

Start Date

October 31, 1995

Conditions
Ornithine Transcarbamylase Deficiency Disease
Interventions
GENETIC

recombinant adenovirus containing the ornithine transcarbamylase gene

All Listed Sponsors
collaborator

Children's National Research Institute

OTHER

lead

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

NIH