Gene Therapy for the Treatment of Fanconi's Anemia Type C

PHASE1CompletedINTERVENTIONAL
Enrollment

9

Participants

Timeline

Start Date

December 3, 1993

Study Completion Date

February 11, 2009

Conditions
Fanconi's AnemiaPancytopenia
Interventions
DRUG

Transduced CD34+ Cells

Trial Locations (1)

20892

National Institutes of Health Clinical Center, 9000 Rockville Pike, Bethesda

All Listed Sponsors
lead

National Heart, Lung, and Blood Institute (NHLBI)

NIH