Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study

CompletedOBSERVATIONAL
Enrollment

10

Participants

Timeline

Start Date

September 30, 1990

Study Completion Date

July 31, 2002

Conditions
Severe Combined Immunodeficiency
Interventions
DRUG

ADA PBSC

DRUG

ADA Umbilical Cord Blood Cells

DRUG

Transduced Lymphocytes

Trial Locations (1)

20892

National Human Genome Research Institute (NHGRI), Bethesda

All Listed Sponsors
lead

National Human Genome Research Institute (NHGRI)

NIH