Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells

PHASE1CompletedINTERVENTIONAL
Enrollment

120

Participants

Timeline

Start Date

January 31, 1988

Study Completion Date

April 30, 2002

Conditions
Gaucher's Disease
Interventions
GENETIC

human glucocerebrosidase cDNA

Trial Locations (1)

20892

National Institute of Neurological Disorders and Stroke (NINDS), Bethesda

All Listed Sponsors
lead

National Institute of Neurological Disorders and Stroke (NINDS)

NIH

NCT00001234 - Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells | Biotech Hunter | Biotech Hunter