About
Protein replacement via Gene Therapy
Areas of Focus
Categories
Gene Therapy, RNA & Peptide Therapy
Team (9)
Clinical Trials (7)
View allTotal Trials
7
As Lead Sponsor
7
As Collaborator
0
Total Enrollment
152
By Phase
PHASE1/PHASE2: 5PHASE1: 1
By Status
TERMINATED: 3COMPLETED: 2RECRUITING: 1ACTIVE_NOT_RECRUITING: 1
Clinical Trials Pipeline7 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2017
2018
2019
2020
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
Today
Hover over trial bars to see details
Recent Trials
NCT06545136Lead Sponsor
Long Term Follow-up Study of Type-1 Gaucher Subjects Post FLT201 Dose (GALILEO-2)
PHASE1/PHASE2Recruiting
75 participants
Started: May 13, 2024 · Completed: May 31, 2029
NCT05324943Lead Sponsor
A Gene Therapy Study in Patients With Gaucher Disease Type 1
PHASE1Active, not recruiting
18 participants
Started: Apr 15, 2022 · Completed: Jul 31, 2025
NCT05164471Lead Sponsor
Phase 1/2 Dose Confirmation Study of FLT180a in Hemophilia B
PHASE1/PHASE2Terminated
6 participants
Started: Dec 6, 2021 · Completed: May 31, 2023
NCT04455230Lead Sponsor
A Long Term Follow-Up Study of Fabry Disease Subjects Treated With FLT190
PHASE1/PHASE2Completed
3 participants
Started: Sep 8, 2020 · Completed: Sep 28, 2023
NCT04272554Lead Sponsor
AAV Gene Therapy Screening/Observational Protocol (ECLIPSE)
N/ACompleted
37 participants
Started: Feb 14, 2020 · Completed: Oct 10, 2022
Locations (1)
Headquarters
Stevenage, UK
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