About
Small Molecules for Protein Misfolding diseases
Areas of Focus
Categories
Small Molecule Pharmaceutical
Clinical Trials (2)
View allTotal Trials
2
As Lead Sponsor
2
As Collaborator
0
Total Enrollment
26
By Status
TERMINATED: 1AVAILABLE: 1
Clinical Trials Pipeline1 trial
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2019
2020
2021
2022
2023
Today
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Recent Trials
NCT04506619Lead Sponsor
Safety and Efficacy Outcomes Following Previously Administered Short-Term Treatment With SHP607 in Extremely Premature Infants
N/ATerminated
26 participants
Started: Sep 9, 2020 · Completed: Aug 5, 2022
NCT07136454Lead Sponsor
Expanded Access/Compassionate Use of Rugonersen in Patients With Angelman Syndrome
N/AAVAILABLE
Locations (1)
Headquarters
Cheshire, UK
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