Gene Therapy
Total Trials
2
As Lead Sponsor
1
As Collaborator
Total Enrollment
12,024
NCT03047369
The Myelin Disorders Biorepository Project
Phase: N/A
Role: Collaborator
Start: Dec 8, 2016
Completion: Dec 8, 2030
NCT04833907
rAAV-Olig001-ASPA Gene Therapy for Treatment of Children With Typical Canavan Disease
Phase: Phase 1/2
Role: Lead Sponsor
Start: Apr 1, 2021
Completion: Aug 31, 2027
Loading map...