Gene Correction Technology
Total Trials
1
As Lead Sponsor
As Collaborator
0
Total Enrollment
15
NCT04819841
Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease
Phase: Phase 1/2
Role: Lead Sponsor
Start: Nov 15, 2021
Completion: Dec 31, 2028
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