Defunct Company
Total Trials
3
As Lead Sponsor
1
As Collaborator
2
Total Enrollment
119
NCT04937062
Phenylbutyrate for Monogenetic Developmental and Epileptic Encephalopathy
Phase: Early Phase 1
Role: Collaborator
Start: Mar 1, 2021
Completion: Dec 31, 2025
NCT05565768
Study to Evaluate HZN-457 in Healthy Volunteers
Phase: Phase 1
Role: Lead Sponsor
Start: Nov 22, 2022
Completion: Aug 9, 2023
NCT06212245
A Clinical Research Study of Inebilizumab in Neuromyelitis Optica Spectrum Disorders
Phase: Phase 4
Start: Feb 25, 2024
Completion: Jun 25, 2025