Defunct Company
Total Trials
2
As Lead Sponsor
As Collaborator
0
Total Enrollment
37
NCT04732429
Study of HST5040 in Subjects With Propionic or Methylmalonic Acidemia
Phase: Phase 2
Role: Lead Sponsor
Start: Mar 15, 2021
Completion: Oct 20, 2023
NCT05438485
Natural History Study of Patients With Methylmalonic Acidemia and Propionic Acidemia
Phase: N/A
Start: Aug 27, 2021