About
AAV Gene Therapy
Areas of Focus
Categories
Virus TechnologyGene Therapy, RNA & Peptide TherapySan Diego & Southern California
Clinical Trials (3)
View allTotal Trials
3
As Lead Sponsor
3
As Collaborator
0
Total Enrollment
43
By Phase
PHASE1/PHASE2: 2
By Status
SUSPENDED: 2WITHDRAWN: 1
Clinical Trials Pipeline3 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2023
2024
2025
2026
2027
2028
2029
2030
Today
Hover over trial bars to see details
Recent Trials
NCT07011771Lead Sponsor
A Clinical Trial of CAP-003 Gene Therapy in Adult Patients With GBA1 Associated Parkinson's Disease
PHASE1/PHASE2Suspended
31 participants
Started: Aug 18, 2025 · Completed: Nov 30, 2029
NCT06983158Lead Sponsor
A Clinical Trial of CAP-002 Gene Therapy in Pediatric Patients With Syntaxin-Binding Protein 1 (STXBP1) Encephalopathy
PHASE1/PHASE2Suspended
12 participants
Started: Jul 3, 2025 · Completed: Dec 20, 2028
NCT05462054Lead Sponsor
Natural History Study in Pediatric Patients with STXBP1 Encephalopathy with Epilepsy
N/AWithdrawn
Started: Oct 31, 2024 · Completed: Jan 31, 2026
Locations (1)
Headquarters
Thousand Oaks, CA, United States
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