About
Gene Therapies targeting neuromuscular diseases
Areas of Focus
Categories
Gene Therapy, RNA & Peptide Therapy
Clinical Trials (3)
View allTotal Trials
3
As Lead Sponsor
3
As Collaborator
0
Total Enrollment
12
By Phase
PHASE1/PHASE2: 1PHASE1: 1
By Status
RECRUITING: 1WITHDRAWN: 1ACTIVE_NOT_RECRUITING: 1
Clinical Trials Pipeline3 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
2031
2032
Today
Hover over trial bars to see details
Recent Trials
NCT05973630Lead Sponsor
ATA-200 Dose-escalation Gene Therapy Trial in Patients With LGMDR5
PHASE1/PHASE2Recruiting
6 participants
Started: Feb 15, 2025 · Completed: Jan 31, 2031
NCT06210672Lead Sponsor
Natural History Study in Patients With LGMDR5/2c
N/AWithdrawn
Started: Jan 10, 2025 · Completed: Sep 1, 2025
NCT05224505Lead Sponsor
ATA-100 (Formerly GNT0006) Gene Therapy Trial in Patients With LGMDR9
PHASE1Active, not recruiting
6 participants
Started: Sep 1, 2022 · Completed: Sep 30, 2029
Locations (1)
Headquarters
Evry, France
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