Gene Therapy
Total Trials
2
As Lead Sponsor
As Collaborator
0
Total Enrollment
96
NCT04126005
Natural History Study of Patients With Canavan Disease (CANinform Study)
Phase: N/A
Role: Lead Sponsor
Start: Oct 10, 2019
Completion: Jul 31, 2025
NCT04998396
A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
Phase: Phase 1/2
Start: Sep 8, 2021
Completion: Oct 8, 2030
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