Defunct Company
Total Trials
2
As Lead Sponsor
As Collaborator
0
Total Enrollment
15
NCT04141670
S 48168 (ARM 210) for the Treatment of RYR1-related Myopathies (RYR1-RM)
Phase: Phase 1
Role: Lead Sponsor
Start: Aug 25, 2020
Completion: Jul 30, 2023
NCT05122975
Treatment of an Inherited Ventricular Arrhythmia
Phase: Phase 2
Start: Aug 1, 2023
Completion: Apr 1, 2024