Personalized Antisense Oligonucleotide for a Single Participant With MAPK8IP3 Neurodevelopmental Disorder With or Without Variable Brain Abnormalities (NEDBA)

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

1

Participants

Timeline

Start Date

February 24, 2025

Primary Completion Date

February 28, 2027

Study Completion Date

February 28, 2027

Conditions
Neurodevelopmental Disorder With or Without Variable Brain Abnormalities
Interventions
DRUG

nL-MAPK8-001

Personalized antisense oligonucleotide

Trial Locations (1)

10032

Columbia University, New York

All Listed Sponsors
collaborator

Columbia University

OTHER

lead

n-Lorem Foundation

OTHER

NCT07197294 - Personalized Antisense Oligonucleotide for a Single Participant With MAPK8IP3 Neurodevelopmental Disorder With or Without Variable Brain Abnormalities (NEDBA) | Biotech Hunter | Biotech Hunter