A Study of SGT-501 Gene Therapy in Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT)

PHASE1Not yet recruitingINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

November 1, 2025

Primary Completion Date

June 30, 2027

Study Completion Date

May 31, 2031

Conditions
Catecholaminergic Polymorphic Ventricular Tachycardia
Interventions
DRUG

SGT-501

IV for infusion

Trial Locations (4)

19104

University of Pennsylvania, Philadelphia

44195

Cleveland Clinic, Cleveland

55905

Mayo Clinic, Rochester

02459

Boston Children's Hospital, Boston

All Listed Sponsors
lead

Solid Biosciences Inc.

INDUSTRY