45
Participants
Start Date
October 30, 2025
Primary Completion Date
August 8, 2027
Study Completion Date
August 8, 2027
S-606001
S-606001 administered orally
Placebo
S-606001 matching placebo administered orally
University of Pittsburgh School of Medicine, Pittsburgh
University of Pennsylvania, Philadelphia
Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax
Duke University Medical Center, Durham
Emory University Hospital, Atlanta
University of Florida (UF) - Gainesville, Gainesville
Cincinnati Children's Hospital Medical Center, Cincinnati
Washington University in St. Louis, St Louis
University of California - Irvine Medical Center, Irvine
UZ Leuven, Leuven
Aarhus University Hospital, Aarhus
HCL Hopital Pierre Wertheimer, Bron
AP-HP Hopital Raymond Poincare, Garches
Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille
CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice
Universitaetsklinikum Halle (Saale), Halle
SphinCS GmbH, Höchheim
Klinikum der Ludwig-Maximilians-Universitaet Muenchen, München
"A.O.U. Policlinico G. Martino", Messina
AOU Citta della Salute e della Scienza di Torino - Ospedale le Molinette, Torino
Erasmus MC, GE Rotterdam
Hospital Universitario 12 de Octubre, Madrid
Hospital Universitari i Politecnic La Fe, Valencia
Queen Elizabeth Hospital Birmingham, Birmingham
National Hospital for Neurology & Neurosurgery, London
Royal Free London NHS Foundation Trust, London
Royal Victoria Infirmary, Newcastle upon Tyne
Salford Royal Hospital, Salford
Lead Sponsor
Shionogi
INDUSTRY