10
Participants
Start Date
August 1, 2025
Primary Completion Date
August 31, 2026
Study Completion Date
August 31, 2027
Eliglustat
Drug: GM-CSF + Eliglustat Granulocyte-Macrophage Colony Stimulating Factor (GM-CSF) and GSL Synthetase Inhibitor
Biotherapeutic Department and Hematology Department of Chinese PLA General Hospital, Beijing
Department of Pediatrics, The First Medical Center, Chinese PLA General Hospital, Beijing
Chinese PLA General Hospital
OTHER