140
Participants
Start Date
June 20, 2025
Primary Completion Date
December 31, 2040
Study Completion Date
December 31, 2040
Vosoritide
Open-label administration of vosoritide using weight-band dosing
Murdoch Children's Research Institute, Parkville
Nemours Children's Hospital, Delaware (Alfred I. Dupont Hospital for Children), Wilmington
Children's National Medical Center, Washington D.C.
Medical College of Wisconsin, Milwaukee
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
University of Alberta Stollery Children's Hospital, Edmonton
SickKids - The Hospital for Sick Children, Toronto
Centre Hospitalier Universitaire Sainte-Justine, Montreal
Hospices Civils de Lyon - Hopital Femme Mere Enfant, Lyon
Hopital de la Timone, Marseille
Hopital Necker-Enfants Malade, Paris
CHU de Toulouse, Toulouse
Uniklinik Koln, Cologne
Univeristatskinderklinik Magdeburg, Magdeburg
Instituto Giannina Gaslini, Genoa
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Rome
Ospedale Pediatrico Bambino Gesu, Rome
Osaka University Hosptial, Osaka
Tokushima University Hospital, Tokushima
Institute of Science Tokyo Hospital, Tokyo
Tottori University Hospital, Tottori
Vithas Hospital San Jose, Vitoria-Gasteiz
Great Ormond Street Hospital for Children NHS Foundation Trust, London
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY