A Multi-center, Ambispective Cohort Study to Evaluate the Impact of Iptacopan for Adult Patients With PNH in China

RecruitingOBSERVATIONAL
Enrollment

80

Participants

Timeline

Start Date

June 10, 2025

Primary Completion Date

April 20, 2027

Study Completion Date

April 20, 2027

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

LNP023

Capsules for oral administration

Trial Locations (1)

300052

RECRUITING

Novartis Investigative Site, Tianjin

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY