First-in-Human Clinical Trial of STUP-001, an In Vivo Direct Cell Conversion Gene Therapy for AIS-A/B Chronic Spinal Cord Injury

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

9

Participants

Timeline

Start Date

July 30, 2025

Primary Completion Date

December 31, 2026

Study Completion Date

December 31, 2027

Conditions
Spinal Cord InjuryChronic Spinal Cord Injury
Interventions
DRUG

STUP-001

in vivo direct cell conversion gene therapy investigational product

Trial Locations (1)

Unknown

RECRUITING

Severance Hospital, Seoul

All Listed Sponsors
collaborator

Stand Up Therapeutics INC.

INDUSTRY

lead

Yonsei University

OTHER